Lentiviral gene therapy with reduced-intensity conditioning for sickle cell disease: a phase 1/2 trial
采用减低强度预处理的慢病毒基因疗法治疗镰状细胞病:一项 1/2 期试验
期刊:Nature Medicine
影响因子:50
doi:10.1038/s41591-025-03662-2
Grimley, Michael; Davies, Stella M; Shrestha, Archana; Shova, Amy; Asnani, Monika; Kent, Michael; Sayani, Farzana; Quinn, Charles T; Niss, Omar; Lutzko, Carolyn; Mehta, Parinda A; Khandelwal, Pooja; Little, Courtney; Chandra, Sharat; Felker, Sydney; Chi, Mengna; Kalfa, Theodosia A; Knight-Madden, Jennifer; Arumugam, Paritha I; Ramos, Kristie N; Witting, Scott; Latham, Teresa; Bushman, Frederic D; Malik, Punam