日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Recruitment and retention of young adults with sickle cell disease

招募和留住患有镰状细胞病的年轻人

Belton, Tanisha; Carbaugh, Lane; Stevens, Evelyn; Seide, Abigail; Ferreira, Bianca; Teng, Olivia; Bennett, Laura; Pfeiffer, Amanda; Ferreira, Mark; Shova, Amy; Arens, Robin; Williford, Desireé N; Aygun, Banu; Appiah-Kubi, Abena; Apollonsky, Nataly; Boruchov, Donna; Niss, Omar; Smith-Whitley, Kim; Jan, Sophia; Steinway, Caren M

Lentiviral gene therapy with reduced-intensity conditioning for sickle cell disease: a phase 1/2 trial

采用减低强度预处理的慢病毒基因疗法治疗镰状细胞病:一项 1/2 期试验

Grimley, Michael; Davies, Stella M; Shrestha, Archana; Shova, Amy; Asnani, Monika; Kent, Michael; Sayani, Farzana; Quinn, Charles T; Niss, Omar; Lutzko, Carolyn; Mehta, Parinda A; Khandelwal, Pooja; Little, Courtney; Chandra, Sharat; Felker, Sydney; Chi, Mengna; Kalfa, Theodosia A; Knight-Madden, Jennifer; Arumugam, Paritha I; Ramos, Kristie N; Witting, Scott; Latham, Teresa; Bushman, Frederic D; Malik, Punam

Community Health Worker and Mobile Health Interventions for Quality of Life Among Young Adults With Sickle Cell Disease: A Randomized Clinical Trial

社区卫生工作者和移动医疗干预对镰状细胞病青年患者生活质量的影响:一项随机临床试验

Jan, Sophia; Steinway, Caren; Belton, Tanisha; Shults, Justine; Bennett, Laura; Teng, Olivia; Griffis, Heather; Aygun, Banu; Appiah-Kubi, Abena; Apollonsky, Nataly; Boruchov, Donna; Niss, Omar; Schwartz, Lisa; Crosby, Lori; Barakat, Lamia; Andemariam, Biree; Mulchan, Siddika S; Rubin, David; Smith-Whitley, Kim

The Community Health Workers and Mobile Health for Emerging Adults Transitioning Sickle Cell Disease Care (COMETS) Trial: Protocol for a Randomized Controlled Trial

社区卫生工作者和移动医疗服务为镰状细胞病成年过渡期患者提供护理(COMETS)试验:随机对照试验方案

Belton, Tanisha D; Steinway, Caren M; Teng, Olivia; Shults, Justine; Barakat, Lamia P; Aygun, Banu; Appiah-Kubi, Abena; Crosby, Lori E; Niss, Omar; Andemariam, Biree; Schwartz, Lisa A; Luma, Samantha; Smith, Kyle A; Johnson, Tracey B; Rubin, David M; Smith-Whitley, Kim M; Jan, Sophia

Longitudinal changes and predictors of cardiac extracellular volume fraction in sickle cell anemia

镰状细胞贫血症患者心脏细胞外容积分数的纵向变化及预测因素

Niss, Omar; Morin, Cara E; Hashemi, Sassan; Alsaied, Tarek; Lang, Sean M; Taylor, Michael D; Tasset, MacKenzie; Malik, Punam; Quinn, Charles T

Genetic variants in canonical Wnt signaling pathway associated with pediatric immune thrombocytopenia

与儿童免疫性血小板减少症相关的经典Wnt信号通路基因变异

Kim, Taylor Olmsted; Geris, Jennifer M; Flanagan, Jonathan M; Grace, Rachael F; Lambert, Michele P; O'Farrell, Candelaria; Rose, Melissa J; Shimano, Kristin A; Niss, Omar; Neunert, Cindy; Nakano, Taizo A; MacMath, Derek; Dinu, Bogdan; Kirk, Susan E; Neufeld, Ellis J; Despotovic, Jenny M; Scheurer, Michael E; Grimes, Amanda B

Hydroyxurea improves cerebral oxygen saturation in children with sickle cell anemia

羟基脲可改善镰状细胞贫血患儿的脑氧饱和度

Karkoska, Kristine; Quinn, Charles T; Niss, Omar; Pfeiffer, Amanda; Dong, Min; Vinks, Alexander A; McGann, Patrick T

Early initiation of hydroxyurea (hydroxycarbamide) using individualised, pharmacokinetics-guided dosing can produce sustained and nearly pancellular expression of fetal haemoglobin in children with sickle cell anaemia

在镰状细胞贫血症患儿中,早期采用个体化的、药代动力学指导的羟基脲(羟基脲)给药方案,可使胎儿血红蛋白持续且几乎在全细胞范围内表达。

Quinn, Charles T; Niss, Omar; Dong, Min; Pfeiffer, Amanda; Korpik, Jennifer; Reynaud, Mary; Bonar, Holly; Kalfa, Theodosia A; Smart, Luke R; Malik, Punam; Ware, Russell E; Vinks, Alexander A; McGann, Patrick T

Congenital dyserythropoietic anemia type I: First report from the Congenital Dyserythropoietic Anemia Registry of North America (CDAR)

先天性红细胞生成障碍性贫血 I 型:来自北美先天性红细胞生成障碍性贫血登记处 (CDAR) 的首份报告

Niss, Omar; Lorsbach, Robert B; Berger, Mikaela; Chonat, Satheesh; McLemore, Morgan; Buchbinder, David; McCavit, Timothy; Shaffer, Linda G; Simpson, Jessica; Schwartz, Jeffrey H; Meznarich, Jessica; Emberesh, Myesa; Seu, Katie G; Zhang, Wenying; Kalfa, Theodosia A

Progression of albuminuria in patients with sickle cell anemia: a multicenter, longitudinal study.

镰状细胞贫血患者蛋白尿进展:一项多中心纵向研究

Niss Omar, Lane Adam, Asnani Monika R, Yee Marianne E, Raj Ashok, Creary Susan, Fitzhugh Courtney, Bodas Prasad, Saraf Santosh L, Sarnaik Sharada, Devarajan Prasad, Malik Punam