WiTNNess: An international natural history study of infantile-onset TNNT1 myopathy
WiTNNess:一项关于婴儿期发病的TNNT1肌病的国际自然史研究
期刊:Annals of Clinical and Translational Neurology
影响因子:3.9
doi:10.1002/acn3.51884
Strauss, Kevin A; Carson, Vincent J; Bolettieri, Emilienne; Everett, Mariah; Bollinger, Ashton; Bowser, Lauren E; Beiler, Keturah; Young, Millie; Edvardson, Simon; Fraenkel, Nitay; D'Amico, Adele; Bertini, Enrico; Lingappa, Lokesh; Chowdhury, Devyani; Lowes, Linda P; Iammarino, Megan; Alfano, Lindsay N; Brigatti, Karlla W