日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Precise correction of a spectrum of β-thalassemia mutations in coding and non-coding regions by base editors

碱基编辑器精确校正编码和非编码区域中的一系列 β-地中海贫血突变

Kirti Prasad, Nivedhitha Devaraju, Anila George, Nithin Sam Ravi, Joshua Paul, Gokulnath Mahalingam, Vignesh Rajendiran, Lokesh Panigrahi, Vigneshwaran Venkatesan, Kartik Lakhotiya, Yogapriya Periyasami, Aswin Anand Pai, Yukio Nakamura, Ryo Kurita, Poonkuzhali Balasubramanian, Saravanabhavan Thangav

Identification of novel HPFH-like mutations by CRISPR base editing that elevate the expression of fetal hemoglobin

利用 CRISPR 碱基编辑技术鉴定可提高胎儿血红蛋白表达的新型 HPFH 样突变

Nithin Sam Ravi ,Beeke Wienert ,Stacia K Wyman ,Henry William Bell ,Anila George ,Gokulnath Mahalingam ,Jonathan T Vu ,Kirti Prasad ,Bhanu Prasad Bandlamudi ,Nivedhitha Devaraju ,Vignesh Rajendiran ,Nazar Syedbasha ,Aswin Anand Pai ,Yukio Nakamura ,Ryo Kurita ,Muthuraman Narayanasamy ,Poonkuzhali Balasubramanian ,Saravanabhavan Thangavel ,Srujan Marepally ,Shaji R Velayudhan ,Alok Srivastava ,Mark A DeWitt ,Merlin Crossley ,Jacob E Corn ,Kumarasamypet M Mohankumar

Efficient and error-free correction of sickle mutation in human erythroid cells using prime editor-2

使用 prime editor-2 高效无误地校正人类红系细胞中的镰状突变

Anila George, Nithin Sam Ravi, Kirti Prasad, Lokesh Panigrahi, Sanya Koikkara, Vignesh Rajendiran, Nivedhitha Devaraju, Joshua Paul, Aswin Anand Pai, Yukio Nakamura, Ryo Kurita, Poonkuzhali Balasubramanian, Saravanabhavan Thangavel, Srujan Marepally, Shaji R Velayudhan, Alok Srivastava, Kumarasamype

Erythroid lineage-specific lentiviral RNAi vectors suitable for molecular functional studies and therapeutic applications

适用于分子功能研究和治疗应用的红细胞谱系特异性慢病毒 RNAi 载体

Abhirup Bagchi #, Nivedhitha Devaraju #, Karthik Chambayil, Vignesh Rajendiran, Vigneshwaran Venkatesan, Nilofer Sayed, Aswin Anand Pai, Aneesha Nath, Ernest David, Yukio Nakamura, Poonkuzhali Balasubramanian, Alok Srivastava, Saravanabhavan Thangavel, Kumarasamypet M Mohankumar, Shaji R Velayudhan1