日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV9 gene therapy optimization for SMARD1/CMT2S: safety and long-term efficacy comparison of two vectors in a SMARD1 preclinical model

针对SMARD1/CMT2S的AAV9基因治疗优化:在SMARD1临床前模型中比较两种载体的安全性和长期疗效

Pagliari, Elisa; Anastasia, Alessia; Bellandi, Floriana; Garbellini, Manuela; Ongaro, Jessica; Taiana, Michela; Comi, Giacomo P; Ottoboni, Linda; Sierra-Delgado, Julieth Andrea; Likhite, Shibi; Meyer, Kathrin C; Nizzardo, Monica; Corti, Stefania P

Targeted antisense oligonucleotide treatment rescues developmental alterations in spinal muscular atrophy organoids

靶向反义寡核苷酸治疗可挽救脊髓性肌萎缩症类器官的发育异常

Irene Faravelli #,Paola Rinchetti #,Monica Tambalo #,Illia Simutin,Lisa Mapelli,Sara Mancinelli,Matteo Miotto,Mafalda Rizzuti,Andrea D'Angelo,Chiara Cordiglieri,Giulia Forotti,Clelia Peano,Paolo Kunderfranco,Luca Calandriello,Giacomo P Comi,Elvezia Paraboschi,Eleonora Pali,Francesca Beatrice,Egidio D'Angelo,Serge Przedborski,Monica Nizzardo,Simona Lodato,Stefania Corti

Oxidative Stress and Semen Quality Among Night- and Day-Shift Workers: A Cross-Sectional Study

夜班和白班工人氧化应激与精液质量:一项横断面研究

Boeri, Luca; Passarelli, Federica; Basadonna, Ludovico Maria; Sorba, Edoardo; Graps, Giorgio; Ciamarra, Fabio; Dagnino, Damiano; Parolin, Valentina; Nizzardo, Marco; Lucignani, Gianpaolo; Montanari, Emanuele

iPSC-derived human cortical organoids display profound alterations of cellular homeostasis following SARS-CoV-2 infection and Spike protein exposure

iPSC衍生的人类皮质类器官在SARS-CoV-2感染和刺突蛋白暴露后表现出细胞稳态的显著改变

Gioia Cappelletti ,Lorenzo Brambilla ,Sergio Strizzi ,Fiona Limanaqi ,Valentina Melzi ,Mafalda Rizzuti ,Monica Nizzardo ,Irma Saulle ,Daria Trabattoni ,Stefania Corti ,Mario Clerici ,Mara Biasin

Targeting STMN2 for neuroprotection and neuromuscular recovery in Spinal Muscular Atrophy: evidence from in vitro and in vivo SMA models

靶向STMN2在脊髓性肌萎缩症的神经保护和神经肌肉恢复中的作用:来自体外和体内SMA模型的证据

Pagliari, Elisa; Taiana, Michela; Manzini, Paolo; Sali, Luca; Quetti, Lorenzo; Bertolasi, Letizia; Oldoni, Samanta; Melzi, Valentina; Comi, Giacomo; Corti, Stefania; Nizzardo, Monica; Rizzo, Federica

Transient ureteral obstruction after mini-percutaneous nephrolithotomy is associated with stone volume and location: results from a single-center, real-life study

微创经皮肾镜取石术后短暂性输尿管梗阻与结石体积和位置相关:一项单中心真实世界研究的结果

Nizzardo, Marco; Zanetti, Stefano Paolo; Marmiroli, Andrea; Lucignani, Gianpaolo; Turetti, Matteo; Silvani, Carlo; Gadda, Franco; Longo, Fabrizio; De Lorenzis, Elisa; Albo, Giancarlo; Salonia, Andrea; Montanari, Emanuele; Boeri, Luca

Vacuum-assisted mini-percutaneous nephrolithotomy is associated with lower rates of infectious complications compared to vacuum-cleaner procedure in patients at high risk for infections: a single-center experience

单中心经验表明,对于感染高风险患者,真空辅助微创经皮肾镜取石术与真空吸石术相比,感染并发症发生率更低:

Marmiroli, Andrea; Nizzardo, Marco; Zanetti, Stefano Paolo; Lucignani, Gianpaolo; Turetti, Matteo; Silvani, Carlo; Gadda, Franco; Longo, Fabrizio; De Lorenzis, Elisa; Albo, Giancarlo; Salonia, Andrea; Montanari, Emanuele; Boeri, Luca

Characterization and translational development of IOA-289, a novel autotaxin inhibitor for the treatment of solid tumors

新型自泌素抑制剂IOA-289的特性分析及转化开发,用于治疗实体瘤

Deken, M A; Niewola-Staszkowska, K; Peyruchaud, O; Mikulčić, N; Antolić, M; Shah, P; Cheasty, A; Tagliavini, A; Nizzardo, A; Pergher, M; Ziviani, L; Milleri, S; Pickering, C; Lahn, M; van der Veen, L; Di Conza, G; Johnson, Z

Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model

细胞穿透肽结合吗啉在有症状的临床前模型中挽救 SMA

Margherita Bersani, Mafalda Rizzuti, Elisa Pagliari, Manuela Garbellini, Domenica Saccomanno, Hong M Moulton, Nereo Bresolin, Giacomo P Comi, Stefania Corti, Monica Nizzardo

Insights into the identification of a molecular signature for amyotrophic lateral sclerosis exploiting integrated microRNA profiling of iPSC-derived motor neurons and exosomes

利用iPSC衍生运动神经元和外泌体的整合microRNA谱分析,深入了解肌萎缩侧索硬化症的分子特征

Rizzuti, Mafalda; Melzi, Valentina; Gagliardi, Delia; Resnati, Davide; Meneri, Megi; Dioni, Laura; Masrori, Pegah; Hersmus, Nicole; Poesen, Koen; Locatelli, Martina; Biella, Fabio; Silipigni, Rosamaria; Bollati, Valentina; Bresolin, Nereo; Comi, Giacomo Pietro; Van Damme, Philip; Nizzardo, Monica; Corti, Stefania