日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A humanized engineered heart tissue platform for cardiotoxicity assessment

用于心脏毒性评估的人源化工程心脏组织平台

Sun, Yao-Hui; Diloretto, Daphne A; Kao, Hillary K J; Sirish, Padmini; Morisseau, Christophe; Sule, Rasheed; Hsu, Ming-Fo; Smithers, Regan L; Overton, James; Timofeyev, Valeriy; Merleev, Alexander; Grigorean, Gabriela; Phinney, Brett S; Maverakis, Emanual M; Gomes, Aldrin V; Haj, Fawaz G; Nolta, Jan A; Chan, James W; Hammock, Bruce D; Lieu, Deborah K; Chiamvimonvat, Nipavan

Randomized Study of Intravitreal Autologous CD34+ Stem Cells in Central Retinal Vein Occlusion (Treatment of Retinal vein occlusion Using STem cells [TRUST] Report 1): Safety and Feasibility

玻璃体内注射自体CD34+干细胞治疗中心性视网膜静脉阻塞的随机研究(干细胞治疗视网膜静脉阻塞[TRUST]报告1):安全性和可行性

Park, Susanna S; McCormack, Jennifer; Salazar, Dagmar; King, Jacquie S; Salvador, Marisa; Bauer, Gerhard; Fury, Brian; Abedi, Mehrdad; Moshiri, Ala; Macias, Denise; Moussa, Kareem; Kondapaka, Radhika; Lindblad, Robert; Hoeg, Rasmus; Nolta, Jan A

Durable HTT silencing using non-evolved dCas9 epigenome editors in patient-derived cells.

利用非进化型 dCas9 表观基因组编辑器在患者来源细胞中实现持久的 HTT 沉默

Waldo Jennifer J, Halmai Julian A N M, Singh Ankita, Gonzalez Casiana E, Chen Yi-An, Carthen Shaylyn A, Nolta Jan A, Fink Kyle D

Investigational New Drug-enabling studies to use genetically modified mesenchymal stromal cells in patients with critical limb ischemia

研究性新药:利用基因修饰的间充质干细胞治疗严重肢体缺血患者的临床研究

Cressman, Amin; Le, Bryan; Morales, David; Yen, Won-Shin; Wu, Fang-Ju; Perotti, Nicholas H; Fury, Brian; Nolta, Jan A; Fierro, Fernando A

Phase I Study of Intravitreal Injection of Autologous CD34+ Stem Cells from Bone Marrow in Eyes with Vision Loss from Retinitis Pigmentosa

自体骨髓CD34+干细胞玻璃体内注射治疗视网膜色素变性引起的视力丧失的I期研究

Park, Susanna S; Bauer, Gerhard; Fury, Brian; Abedi, Mehrdad; Perotti, Nicholas; Colead-Bergum, Dane; Nolta, Jan A

A de novo missense mutation in PPP2R5D alters dopamine pathways and morphology of iPSC-derived midbrain neurons.

PPP2R5D 中的新生错义突变改变了 iPSC 衍生的中脑神经元的多巴胺通路和形态

Carter Jasmine L, Halmai Julian A N M, Waldo Jennifer J, Vij Paula A, Anguiano Maribel, Villegas Isaac J, Du Yu Xin, Nolta Jan, Fink Kyle D

Long-Term Engraftment of Cryopreserved Human Neurons for In Vivo Disease Modeling in Neurodegenerative Disease.

冷冻保存的人类神经元长期移植用于神经退行性疾病的体内疾病建模

Marmion David J, Deng Peter, Hiller Benjamin M, Lewis Rachel L, Harms Lisa J, Cameron David L, Nolta Jan A, Kordower Jeffrey H, Fink Kyle D, Wakeman Dustin R

Delphi-driven consensus definition for mesenchymal stromal cells and clinical reporting guidelines for mesenchymal stromal cell-based therapeutics

基于德尔菲法的间充质干细胞共识定义及间充质干细胞疗法的临床报告指南

Renesme, Laurent; Cobey, Kelly D; Lalu, Manoj M; Bubela, Tania; Chinnadurai, Raghavan; De Vos, John; Dunbar, Rod; Fergusson, Dean; Freund, Daniel; Galipeau, Jacques; Horwitz, Edwin; Lê, Maxime; Matthay, Michael; Moher, David; Nolta, Jan; Parker, Graham; Phinney, Donald G; Rao, Mahendra; Rasko, John E J; Rocco, Patricia R M; Rossi, Fabio; Myles, Michael Rosu; Viswanathan, Sowmya; Thébaud, Bernard

MSCs mediate long-term efficacy in a Crohn's disease model by sustained anti-inflammatory macrophage programming via efferocytosis

MSCs 通过胞吐作用持续发挥抗炎巨噬细胞编程作用,在克罗恩病模型中发挥长期疗效

Maneesh Dave, Atul Dev, Rodrigo A Somoza, Nan Zhao, Satish Viswanath, Pooja Rani Mina, Prathyush Chirra, Verena Carola Obmann, Ganapati H Mahabeleshwar, Paola Menghini, Blythe Durbin-Johnson, Jan Nolta, Christopher Soto, Abdullah Osme, Lam T Khuat, William J Murphy, Arnold I Caplan, Fabio Cominelli

The sinoatrial node extracellular matrix promotes pacemaker phenotype and protects automaticity in engineered heart tissues from cyclic strain.

窦房结细胞外基质促进起搏器表型,并保护工程心脏组织免受周期性应力的影响,从而保持其自律性

Sun Yao-Hui, Kao Hillary K J, Thai Phung N, Smithers Regan, Chang Che-Wei, Pretto Dalyir, Yechikov Sergey, Oppenheimer Sarah, Bedolla Amanda, Chalker Brooke A, Ghobashy Rana, Nolta Jan A, Chan James W, Chiamvimonvat Nipavan, Lieu Deborah K