日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

TFEB coordinates autophagosome biogenesis and ribophagy during starvation via SQSTM1.

TFEB 通过 SQSTM1 在饥饿期间协调自噬体生物合成和核糖体自噬。

Iavazzo Maria, Cinque Laura, Levantovsky Sophie, Morrone Castrese, Monfregola Jlenia, Raimondi Andrea, Polishchuk Elena, De Cegli Rossella, Carrella Diego, Nusco Edoardo, Ferrante Luigi, Sacco Francesca, Frankel Lisa B, Behrends Christian, Settembre Carmine

Impact of liver fibrosis on AAV-mediated gene transfer to mouse hepatocytes

肝纤维化对AAV介导的基因转移至小鼠肝细胞的影响

Ferriero, Rosa; Bruno, Gemma; Padula, Agnese; Pisano, Simone; Boffa, Iolanda; Gargaro, Marco; Imperatore, Teresa; Battipaglia, Maria; Vivenzio, Silvia; Perna, Claudia; Nusco, Edoardo; Ferrante, Luigi; Westhaus, Adrian; Knight, Maddison; Manni, Giorgia; Campione, Severo; Di Napoli, Evaristo; Polishchuk, Elena; Polishchuk, Roman; Paciello, Orlando; Brunetti-Pierri, Nicola; Lisowski, Leszek; Fallarino, Francesca; Piccolo, Pasquale

Combined intraocular and intravenous gene delivery for therapy of gyrate atrophy of the choroid and retina.

眼内和静脉联合基因递送治疗脉络膜和视网膜回旋状萎缩

Dell'Aquila Fabio, Di Cunto Roberto, Marrocco Elena, Del Prete Eugenio, D'Alessio Alfonso, De Stefano Lucia, Notaro Simone, Nusco Edoardo, Auricchio Alberto

TRPML-1 Dysfunction and Renal Tubulopathy in Mucolipidosis Type IV.

TRPML-1 功能障碍与 IV 型粘脂病肾小管病变

Grieco Giuseppina, Montefusco Sandro, Nusco Edoardo, Capuozzo Antonella, Cervellini Francesca, Polishchuk Elena, Bishop Martha, Miele Antonio, D'Apolito Luciano, La Vecchia Claudia, Aurilia Miriam, Schiavo Michela, Staiano Leopoldo, Cesana Marcella, Oberman Rebecca, Lynch Anna V, Musolino Patricia, Trepiccione Francesco, Grishchuk Yulia, Medina Diego Luis

Hepatocyte delivery of miR-34b/c reduces hepatic stellate cell activation and improves liver fibrosis.

肝细胞递送 miR-34b/c 可减少肝星状细胞活化并改善肝纤维化

Piccolo Pasquale, Ferriero Rosa, Perna Claudia, Nusco Edoardo, Monti Marcello, De Cegli Rossella, Barbato Anna, Sorrentino Nicolina Cristina, Viscomi Maria Teresa, Cariello Marica, Moschetta Antonio, Campione Severo, Brunetti-Pierri Nicola

Increased expression or activation of TRPML1 reduces hepatic storage of toxic Z alpha-1 antitrypsin

TRPML1表达或激活增加可减少肝脏中毒性Zα-1抗胰蛋白酶的储存

Pastore, Nunzia; Annunziata, Francesco; Colonna, Rita; Maffia, Veronica; Giuliano, Teresa; Custode, Bruno Maria; Lombardi, Bernadette; Polishchuk, Elena; Cacace, Vincenzo; De Stefano, Lucia; Nusco, Edoardo; Sorrentino, Nicolina Cristina; Piccolo, Pasquale; Brunetti-Pierri, Nicola

The Amyloid Inhibitor CLR01 Relieves Autophagy and Ameliorates Neuropathology in a Severe Lysosomal Storage Disease

淀粉样蛋白抑制剂CLR01可缓解自噬并改善严重溶酶体贮积症的神经病理学症状

Monaco, Antonio; Maffia, Veronica; Sorrentino, Nicolina Cristina; Sambri, Irene; Ezhova, Yulia; Giuliano, Teresa; Cacace, Vincenzo; Nusco, Edoardo; De Risi, Maria; De Leonibus, Elvira; Schrader, Thomas; Klärner, Frank-Gerrit; Bitan, Gal; Fraldi, Alessandro

Low incidence of hepatocellular carcinoma in mice and cats treated with systemic adeno-associated viral vectors.

用全身性腺相关病毒载体治疗的小鼠和猫中肝细胞癌的发生率较低

Ferla Rita, Alliegro Marialuisa, Dell'Anno Margherita, Nusco Edoardo, Cullen John M, Smith Stephanie N, Wolfsberg Tyra G, O'Donnell Patricia, Wang Ping, Nguyen Anh-Dao, Chandler Randy J, Chen Zelin, Burgess Shawn M, Vite Charles H, Haskins Mark E, Venditti Charles P, Auricchio Alberto

Enhancement of hepatic autophagy increases ureagenesis and protects against hyperammonemia

增强肝脏自噬可增加尿素生成并预防高氨血症。

Soria, Leandro R; Allegri, Gabriella; Melck, Dominique; Pastore, Nunzia; Annunziata, Patrizia; Paris, Debora; Polishchuk, Elena; Nusco, Edoardo; Thöny, Beat; Motta, Andrea; Häberle, Johannes; Ballabio, Andrea; Brunetti-Pierri, Nicola

Transcriptional activation of RagD GTPase controls mTORC1 and promotes cancer growth

RagD GTP酶的转录激活调控mTORC1并促进肿瘤生长

Di Malta, Chiara; Siciliano, Diletta; Calcagni, Alessia; Monfregola, Jlenia; Punzi, Simona; Pastore, Nunzia; Eastes, Andrea N; Davis, Oliver; De Cegli, Rossella; Zampelli, Angela; Di Giovannantonio, Luca G; Nusco, Edoardo; Platt, Nick; Guida, Alessandro; Ogmundsdottir, Margret Helga; Lanfrancone, Luisa; Perera, Rushika M; Zoncu, Roberto; Pelicci, Pier Giuseppe; Settembre, Carmine; Ballabio, Andrea