日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Sustained Benefit of Blinatumomab in Infants With KMT2A-Rearranged ALL: Long-Term Outcomes, Toxicity, and Pharmacokinetics

Blinatumomab 对 KMT2A 重排 ALL 患儿的持续疗效:长期结果、毒性和药代动力学

Vieira Martins, Miguel; de Lorenzo, Paola; Kotecha, Rishi S; Attarbaschi, Andishe; Escherich, Gabriele; Nysom, Karsten; Stary, Jan; Ferster, Alina; Brethon, Benoit; Locatelli, Franco; Schrappe, Martin; Scholte-van Houtem, Peggy E; Valsecchi, Maria G; Huitema, Alwin D R; Pieters, Rob; van der Sluis, Inge M

Dinutuximab Beta Added to Temozolomide-Based Chemotherapy for Children With Relapsed and Refractory Neuroblastoma: Results of the ITCC-SIOPEN BEACON Immuno Phase II Trial

Dinutuximab Beta 联合替莫唑胺化疗治疗复发难治性神经母细胞瘤患儿:ITCC-SIOPEN BEACON II 期免疫试验结果

Gray, Juliet C; Weston, Rebekah; Owens, Cormac; Canete, Adela; Gambart, Marion; De Wilde, Bram; Nysom, Karsten; van Eijkelenburg, Natasha; Ladenstein, Ruth; Castellano, Aurora; Gerber, Nicolas U; Marshall, Lynley V; Barone, Giuseppe; Rubio-San-Simon, Alba; Ng, Antony; Vaidya, Sucheta; Gallego, Soledad; Makin, Guy; Burke, G A Amos; McCarthy, Anthony; Murphy, Dermot; Zwaan, C Michel; López-Almaraz, Ricardo; Jannier, Sarah; Thebaud, Estelle; Corradini, Nadege; Yeomanson, Dan; Howell, Lisa; Tweddle, Deborah A; Elliott, Martin; Hobin, Dave; Valteau-Couanet, Dominique; Schleiermacher, Gudrun; Chastagner, Pascal; Defachelles, Anne Sophie; Brichard, Benedicte; George, Sally; Chesler, Louis; Laidler, Jennifer; Firth, Charlotte; Holt, Grace; Moroz, Veronica; Pearson, Andrew D J; Gates, Simon; Wheatley, Keith; Kearns, Pam; Moreno, Lucas

Pathway for the Development of ATR Inhibitors in Pediatric Malignancies: An ACCELERATE Multistakeholder Analysis

儿童恶性肿瘤中ATR抑制剂的研发路径:一项ACCELERATE多方利益相关者分析

Gatz, Susanne A; Glade-Bender, Julia; Pearson, Andrew D J; Ortiz, Michael V; Bernardi, Ronald; Chesler, Lou; Clifford, Steve; Cohen-Gogo, Sarah; De La Cuesta, Esther; de Rojas, Teresa; Durinck, Kaat; Federico, Sara; Fox, Elizabeth; George, Sally; Gounaris, Ioannis; Henssen, Anton George; Irwin, Meredith; Kool, Marcel; Lau, Alan; Nysom, Karsten; Pappo, Alberto; Pennock, Gregory K; Pfister, Stefan M; Scobie, Nicole; Slotkin, Emily K; Smith, Malcolm; Speleman, Frank; Stewart, Elizabeth A; Weigel, Brenda J; Vassal, Gilles

The anti-GD2 monoclonal antibody naxitamab plus GM-CSF for relapsed or refractory high-risk neuroblastoma: a phase 2 clinical trial

抗GD2单克隆抗体naxitamab联合GM-CSF治疗复发或难治性高危神经母细胞瘤:一项II期临床试验

Mora, Jaume; Chan, Godfrey C F; Morgenstern, Daniel A; Amoroso, Loredana; Nysom, Karsten; Faber, Jörg; Wingerter, Arthur; Bear, Melissa K; Rubio-San-Simon, Alba; de Las Heras, Blanca Martínez; Tornøe, Karen; Düring, Maria; Kushner, Brian H

Isatuximab in combination with chemotherapy for pediatric patients with relapsed/refractory acute lymphoblastic leukemia or acute myeloid leukemia: The ISAKIDS study

伊沙妥昔单抗联合化疗治疗复发/难治性急性淋巴细胞白血病或急性髓系白血病患儿:ISAKIDS 研究

Baruchel, André; Nysom, Karsten; Kang, Hyoung Jin; Felice, Maria S; Michalowski, Mariana Bohns; Freigeiro, Daniel; Epelman, Sidnei; Lopes de Sousa, Ana Virginia; Valera, Elvis Terci; Moreira, Larissa; Leverger, Guy; Nelken, Brigitte; Kattamis, Antonis; Rizzari, Carmelo; Fagioli, Franca; Cesaro, Simone; González-Llano, Oscar; Buechner, Jochen; Choque, Willy Quiñones; Duarte, Joaquin; Abrahamsson, Jonas; Alarcón, Ada; Wang, Lynn; Macé, Sandrine; Oprea, Corina; Abbadessa, Giovanni; Zwaan, C Michel

Radiographic and visual response to the type II RAF inhibitor tovorafenib in children with relapsed/refractory optic pathway glioma in the FIREFLY-1 trial

FIREFLY-1试验中,复发/难治性视路胶质瘤患儿对II型RAF抑制剂托沃拉非尼的放射学和视觉反应

Nysom, Karsten; Kilburn, Lindsay B; Leary, Sarah E S; Landi, Daniel B; de Vos-Kerkhof, Evelien; Perreault, Sébastien; Witt, Olaf; Ziegler, David S; Hernáiz Driever, Pablo; Franson, Andrea T; Baxter, Patricia A; Whipple, Nicholas S; Kline, Cassie; Segal, Devorah; Jabado, Nada; Bailey, Simon; McCowage, Geoffrey; Hansford, Jordan R; Khuong-Quang, Dong-Anh; Gottardo, Nicholas G; Hassall, Timothy; Han, Jung Woo; Yalon Oren, Michal; Chi, Susan N; Qiu, Jiaheng; Da Costa, Daniel; Govinda Raju, Sandya; Manley, Peter; Hargrave, Darren

Assessment of peripheral blood DNA methylation signatures as pharmacodynamic and predictive biomarkers during azacitidine therapy in juvenile myelomonocytic leukaemia: Results of the EWOG-MESRAT study

评估外周血DNA甲基化特征作为阿扎胞苷治疗幼年型骨髓单核细胞白血病期间的药效学和预测性生物标志物:EWOG-MESRAT研究结果

Schönung, Maximilian; Rathmann, Silvia; Ramamoorthy, Senthilkumar; Lebrecht, Dirk; Klingebiel, Thomas; Locatelli, Franco; Nysom, Karsten; Rossig, Claudia; Starý, Jan; Zecca, Marco; Patturajan, Meera; Erlacher, Miriam; Strahm, Brigitte; Niemeyer, Charlotte M; Lipka, Daniel B; Flotho, Christian

Glucocorticoid use in paediatric posterior fossa tumour surgery and the occurrence of postoperative speech impairment

糖皮质激素在儿童后颅窝肿瘤手术中的应用及术后言语障碍的发生

Sarup, Rebekka; Laustsen, Aske F; Sørensen, Martin K; Mallucci, Conor; Pizer, Barry; Aquilina, Kristian; Molinari, Emanuela; Hjort, Magnus Aasved; Frič, Radek; Nyman, Per; Sabel, Magnus; Nilsson, Pelle; Matukevičius, Algimantas; Hauser, Peter; Mudra, Katalin; Carai, Andrea; Zipfel, Julian; Hoving, Eelco; van Baarsen, Kirsten; IIIrd, Vladimír Beneš; Peyrl, Andreas; Nysom, Karsten; Sehested, Astrid Marie; Schmiegelow, Kjeld; Juhler, Marianne; Grønbæk, Jonathan K; Mathiesen, René

The type II RAF inhibitor tovorafenib in relapsed/refractory pediatric low-grade glioma: the phase 2 FIREFLY-1 trial

II 型 RAF 抑制剂托沃拉非尼治疗复发/难治性儿童低级别胶质瘤:II 期 FIREFLY-1 试验

Kilburn, Lindsay B; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Landi, Daniel; van der Lugt, Jasper; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Waanders, Angela J; Ziegler, David S; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Hassall, Timothy E; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Yalon Oren, Michal; Toledano, Helen; Larouche, Valérie; Kline, Cassie; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Gerber, Nicolas U; Whipple, Nicholas S; Segal, Devorah; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Cornelio, Izzy; McLeod, Lisa; Zhao, Xin; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Blackman, Samuel C; Packer, Roger J; Nysom, Karsten

Bevacizumab, Irinotecan, or Topotecan Added to Temozolomide for Children With Relapsed and Refractory Neuroblastoma: Results of the ITCC-SIOPEN BEACON-Neuroblastoma Trial

贝伐珠单抗、伊立替康或拓扑替康联合替莫唑胺治疗复发难治性神经母细胞瘤患儿:ITCC-SIOPEN BEACON-神经母细胞瘤试验结果

Moreno, Lucas; Weston, Rebekah; Owens, Cormac; Valteau-Couanet, Dominique; Gambart, Marion; Castel, Victoria; Zwaan, C Michel; Nysom, Karsten; Gerber, Nicolas; Castellano, Aurora; Laureys, Genevieve; Ladenstein, Ruth; Rössler, Jochen; Makin, Guy; Murphy, Dermot; Morland, Bruce; Vaidya, Sucheta; Thebaud, Estelle; van Eijkelenburg, Natasha; Tweddle, Deborah A; Barone, Giuseppe; Tandonnet, Julie; Corradini, Nadege; Chastagner, Pascal; Paillard, Catherine; Bautista, Francisco J; Gallego Melcon, Soledad; De Wilde, Bram; Marshall, Lynley; Gray, Juliet; Burchill, Susan A; Schleiermacher, Gudrun; Chesler, Louis; Peet, Andrew; Leach, Martin O; McHugh, Kieran; Hayes, Roisin; Jerome, Neil; Caron, Hubert; Laidler, Jennifer; Fenwick, Nicola; Holt, Grace; Moroz, Veronica; Kearns, Pamela; Gates, Simon; Pearson, Andrew D J; Wheatley, Keith