Placebo-controlled crossover assessment of mecasermin for the treatment of Rett syndrome
一项安慰剂对照交叉研究评估了美卡司明治疗雷特综合征的疗效
期刊:Annals of Clinical and Translational Neurology
影响因子:3.9
doi:10.1002/acn3.533
O'Leary, Heather M; Kaufmann, Walter E; Barnes, Katherine V; Rakesh, Kshitiz; Kapur, Kush; Tarquinio, Daniel C; Cantwell, Nicole G; Roche, Katherine J; Rose, Suzanne A; Walco, Alexandra C; Bruck, Natalie M; Bazin, Grace A; Holm, Ingrid A; Alexander, Mark E; Swanson, Lindsay C; Baczewski, Lauren M; Poon, Chi‐Sang; Mayor Torres, Juan M; Nelson, Charles A 3rd; Sahin, Mustafa