Blood biodistribution and vector shedding of valoctocogene roxaparvovec in people with severe hemophilia A
重度血友病A患者血液中valoctocogene roxaparvovec的生物分布和载体脱落
期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2024013150
Agarwal, Suresh; Sandza, Krystal; Obrochta Moss, Kristin; Vora, Monica; Bowen, Alisa; Bunch, Brenna; Holcomb, Jennifer; Robinson, Tara M; Jayaram, Kala; Russell, Chris B; Zoog, Stephen; Vettermann, Christian; Henshaw, Joshua