日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Preclinical evaluation of antisense oligonucleotide therapy in a mouse model of HNRNPH2-related neurodevelopmental disorder

在HNRNPH2相关神经发育障碍小鼠模型中对反义寡核苷酸疗法进行临床前评估

Korff, Ane; Yang, Xiaojing; Ozdemir, Ozan; Samanta, Ananya; Wang, Yong-Dong; Patni, Tushar; Lavado, Alfonso J; Kavirayani, Anoop Murthy; Ochaba, Joseph; Powers, Berit; Bennett, C Frank; Kim, Hong Joo; Taylor, J Paul

Measuring digital health literacy in Europe – developing a new tool to capture innovation

衡量欧洲的数字健康素养——开发一种捕捉创新的新工具

Jadali, Zohreh; Doroodgar, Farideh; Bord, S; Paldi, Y; Baruch, R; Stolerman, E; Yeudai-Yadid, M; Zimmerman, D; Gens, I; Schuman Adatto, I; Yaari, M; Khazen, M; Golan Cohen, A; Rose, AJR; Bord, S; Inchi, L; Paldi, Y; Baruch, R; Stolerman, E; Schwartz Shpiro, M; Ronen, S; Eisenberg, L; Yaari, M; Levin-Zamir, D; Arabska, Y; Bíró, É; Krajnovic, D; Le, C; Link, T; Mancini, J; Ochaba, R; Schaeffer, D; Van den Broucke, S

Bedside critical care training: A quasi-experimental study in the paediatric emergency department of a referral hospital in Nigeria

床旁重症监护培训:尼日利亚一家转诊医院儿科急诊科的准实验研究

Abiodun, M T; Ochaba, E A; Kpongo-Ogieva, A

Neural deficits in a mouse model of PACS1 syndrome are corrected with PACS1- or HDAC6-targeting therapy

在PACS1综合征小鼠模型中,针对PACS1或HDAC6的靶向治疗可以纠正神经缺陷。

Sabrina Villar-Pazos # ,Laurel Thomas # ,Yunhan Yang ,Kun Chen ,Jenea B Lyles ,Bradley J Deitch ,Joseph Ochaba ,Karen Ling ,Berit Powers ,Sebastien Gingras ,Holly B Kordasiewicz ,Melanie J Grubisha ,Yanhua H Huang ,Gary Thomas

RNA-targeted therapy corrects neuronal deficits in PACS1 syndrome mice

RNA 靶向治疗可纠正 PACS1 综合征小鼠的神经元缺陷

Sabrina Villar-Pazos, Laurel Thomas, Yunhan Yang, Kun Chen, Jenea B Lyles, Bradley J Deitch, Joseph Ochaba, Karen Ling, Berit Powers, Sebastien Gingras, Holly B Kordasiewicz, Melanie J Grubisha, Yanhua H Huang, Gary Thomas

Factors Associated with Utilization of HIV Testing Services among Adolescents Aged 10-19 Years in Lira District, Northern Uganda: A Cross-Sectional Study

影响乌干达北部利拉区10-19岁青少年艾滋病毒检测服务利用情况的因素:一项横断面研究

Benyumiza, Deo; Amongin, Joan Fidelia; Ochaba, Isaac; Adupa, Morish; Abuch, Naume; Banula, Constance Babirye; Udho, Samson

PIAS1 modulates striatal transcription, DNA damage repair, and SUMOylation with relevance to Huntington's disease

PIAS1 调节纹状体转录、DNA 损伤修复和 SUMO 化,与亨廷顿氏病相关

Eva L Morozko, Charlene Smith-Geater, Alejandro Mas Monteys, Subrata Pradhan, Ryan G Lim, Peter Langfelder, Marketta Kachemov, Jayesh A Kulkarni, Josh Zaifman, Austin Hill, Jennifer T Stocksdale, Pieter R Cullis, Jie Wu, Joseph Ochaba, Ricardo Miramontes, Anirban Chakraborty, Tapas K Hazra, Alice La

Therapeutic efficacy of antisense oligonucleotides in mouse models of CLN3 Batten disease

反义寡核苷酸对CLN3巴顿病小鼠模型的治疗效果

Jessica L Centa, Francine M Jodelka, Anthony J Hinrich, Tyler B Johnson, Joseph Ochaba, Michaela Jackson, Dominik M Duelli, Jill M Weimer, Frank Rigo, Michelle L Hastings

Microglial depletion prevents extracellular matrix changes and striatal volume reduction in a model of Huntington's disease

小胶质细胞耗竭可防止亨廷顿氏病模型中的细胞外基质变化和纹状体体积减少

Joshua D Crapser, Joseph Ochaba, Neelakshi Soni, Jack C Reidling, Leslie M Thompson, Kim N Green

A novel and translational role for autophagy in antisense oligonucleotide trafficking and activity

自噬在反义寡核苷酸运输和活性中的新型转化作用

Ochaba, Joseph; Powers, Andrew F; Tremble, Kaitlyn A; Greenlee, Sarah; Post, Noah M; Matson, John E; MacLeod, A Robert; Guo, Shuling; Aghajan, Mariam