日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Computational normal mode analysis accurately replicates the activity and specificity profiles of CRISPR-Cas9 and high-fidelity variants

计算正态模式分析能够准确地复现 CRISPR-Cas9 及其高保真变体的活性和特异性特征。

Shor, Oded; Rabinowitz, Roy; Offen, Daniel; Benninger, Felix

Single-Base Resolution: Increasing the Specificity of the CRISPR-Cas System in Gene Editing

单碱基分辨率:提高CRISPR-Cas系统在基因编辑中的特异性

Rabinowitz, Roy; Offen, Daniel

Prediction of synonymous corrections by the BE-FF computational tool expands the targeting scope of base editing

利用BE-FF计算工具预测同义突变,扩大了碱基编辑的目标范围。

Rabinowitz, Roy; Abadi, Shiran; Almog, Shiri; Offen, Daniel

Promising Opportunities for Treating Neurodegenerative Diseases with Mesenchymal Stem Cell-Derived Exosomes

利用间充质干细胞来源的外泌体治疗神经退行性疾病的广阔前景

Guy, Reut; Offen, Daniel

A novel specific PERK activator reduces toxicity and extends survival in Huntington's disease models

一种新型特异性PERK激活剂可降低亨廷顿病模型的毒性并延长生存期。

Ganz, Javier; Shacham, Talya; Kramer, Maria; Shenkman, Marina; Eiger, Hagit; Weinberg, Nitai; Iancovici, Ori; Roy, Somnath; Simhaev, Luba; Da'adoosh, Benny; Engel, Hamutal; Perets, Nisim; Barhum, Yael; Portnoy, Moshe; Offen, Daniel; Lederkremer, Gerardo Z

CrisPam: SNP-Derived PAM Analysis Tool for Allele-Specific Targeting of Genetic Variants Using CRISPR-Cas Systems

CrisPam:基于SNP的PAM分析工具,用于利用CRISPR-Cas系统进行等位基因特异性基因变异靶向

Rabinowitz, Roy; Almog, Shiri; Darnell, Roy; Offen, Daniel

Human Muscle Progenitor Cells Overexpressing Neurotrophic Factors Improve Neuronal Regeneration in a Sciatic Nerve Injury Mouse Model.

过表达神经营养因子的人类肌肉祖细胞可改善坐骨神经损伤小鼠模型中的神经元再生

Guy Reut, Grynspan Frida, Ben-Zur Tali, Panski Avraham, Lamdan Ron, Danon Uri, Yaffe David, Offen Daniel

Intranasal administration of exosomes derived from mesenchymal stem cells ameliorates autistic-like behaviors of BTBR mice.

鼻内给药间充质干细胞来源的外泌体可改善 BTBR 小鼠的自闭症样行为

Perets Nisim, Hertz Stav, London Michael, Offen Daniel

Toll-Like Receptor-4 Inhibitor TAK-242 Attenuates Motor Dysfunction and Spinal Cord Pathology in an Amyotrophic Lateral Sclerosis Mouse Model

Toll样受体4抑制剂TAK-242可减轻肌萎缩侧索硬化症小鼠模型中的运动功能障碍和脊髓病理。

Fellner, Avi; Barhum, Yael; Angel, Ariel; Perets, Nisim; Steiner, Israel; Offen, Daniel; Lev, Nirit

A DJ-1 Based Peptide Attenuates Dopaminergic Degeneration in Mice Models of Parkinson's Disease via Enhancing Nrf2

基于 DJ-1 的肽通过增强 Nrf2 来减轻帕金森病小鼠模型中的多巴胺能退化

Lev, Nirit; Barhum, Yael; Ben-Zur, Tali; Aharony, Israel; Trifonov, Lena; Regev, Noa; Melamed, Eldad; Gruzman, Arie; Offen, Daniel