日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Adeno-associated virus expressing a blood-brain barrier-penetrating enzyme improves GM1 gangliosidosis in a preclinical model.

表达血脑屏障穿透酶的腺相关病毒在临床前模型中改善了 GM1 神经节苷脂沉积症

Matsushima Saki Kondo, Shimada Yohta, Kinoshita Masafumi, Nagashima Takashi, Okamoto Shinichiro, Iizuka Sayoko, Takagi Haruna, Iizuka Shunsuke, Higuchi Takashi, Hioki Hiroyuki, Watabe Ayako M, Sonoda Hiroyuki, Ohashi Toya, Kobayashi Hiroshi

Erratum: Hematopoietic stem cell gene therapy ameliorates CNS involvement in murine model of GM1-gangliosidosis

更正:造血干细胞基因疗法可改善GM1神经节苷脂病小鼠模型的中枢神经系统受累情况。

Tsunogai, Toshiki; Ohashi, Toya; Shimada, Yohta; Higuchi, Takashi; Kimura, Ayaka; Watabe, Ayako M; Kato, Fusao; Ida, Hiroyuki; Kobayashi, Hiroshi

Hematopoietic stem cell gene therapy ameliorates CNS involvement in murine model of GM1-gangliosidosis.

造血干细胞基因治疗可改善GM1神经节苷脂病小鼠模型的中枢神经系统受累情况

Tsunogai Toshiki, Ohashi Toya, Shimada Yohta, Higuchi Takashi, Kimura Ayaka, Watabe Ayako M, Kato Fusao, Ida Hiroyuki, Kobayashi Hiroshi

The role of native T1 values on the evaluation of cardiac manifestation in Japanese Fabry disease patients

原生T1值在日本法布里病患者心脏表现评估中的作用

Anan, Ikuko; Sakuma, Toru; Fukuro, Eiko; Morimoto, Satoshi; Nojiri, Ayumi; Kawai, Makoto; Sakurai, Ken; Kobayashi, Masahisa; Kobayashi, Hiroshi; Ida, Hiroyuki; Ohashi, Toya; Yoshimura, Michihiro; Eto, Yoshikatsu; Hongo, Kenichi

IMMU-12. PHASE I/II TRIAL OF IMMUNOTHERAPY WITH FUSIONS OF DENDRITIC CELLS AND TUMOR CELLS FOR RELAPSED OR REFRACTORY BRAIN TUMORS IN CHILDREN AND YOUNG ADULTS

IMMU-12. 针对儿童和青少年复发性或难治性脑肿瘤的树突状细胞与肿瘤细胞融合免疫疗法的 I/II 期试验

Li, Liu-Yu; Zhang, Mei-Qing; Ying, Wen-Min; Zhang, Wen-Zhen; Jiang, Wei-Jing; Xiong, Ting-Jie; Wang, Feng-Mei; Fu, Zhi-Chao; Yamaoka, Masayoshi; Akasaki, Yasuharu; Takei, Jun; Akiyama, Masaharu; Tasaki, Tetsunori; Ohashi, Toya; Ida, Hiroyuki; Yanagisawa, Takaaki

Massive accumulation of globotriaosylceramide in various tissues from a Fabry patient with a high antibody titer against alpha-galactosidase A after 6 years of enzyme replacement therapy

一名法布里病患者在接受酶替代疗法6年后,其多种组织中出现大量三己糖神经酰胺的积累,该患者体内针对α-半乳糖苷酶A的抗体滴度很高。

Hongo, Kenichi; Harada, Toru; Fukuro, Eiko; Kobayashi, Masahisa; Ohashi, Toya; Eto, Yoshikatsu

Efficacy and safety of migalastat in a Japanese population: a subgroup analysis of the ATTRACT study

米格司他在日本人群中的疗效和安全性:ATTRACT 研究的亚组分析

Narita, Ichiei; Ohashi, Toya; Sakai, Norio; Hamazaki, Takashi; Skuban, Nina; Castelli, Jeffrey P; Lagast, Hjalmar; Barth, Jay A

Nafamostat Mesilate Enhances the Radiosensitivity and Reduces the Radiation-Induced Invasive Ability of Colorectal Cancer Cells

萘莫司他甲磺酸盐可增强结直肠癌细胞的放射敏感性并降低其辐射诱导的侵袭能力

Sugano, Hiroshi; Shirai, Yoshihiro; Horiuchi, Takashi; Saito, Nobuhiro; Shimada, Yohta; Eto, Ken; Uwagawa, Tadashi; Ohashi, Toya; Yanaga, Katsuhiko

Glycogen synthase kinase-3β activity plays a key role in the antitumor effect of nafamostat mesilate in pancreatic cancer cells

糖原合成酶激酶-3β活性在萘莫司他甲磺酸盐对胰腺癌细胞的抗肿瘤作用中起关键作用。

Haruki, Koichiro; Shiba, Hiroaki; Shimada, Yohta; Shirai, Yoshihiro; Iwase, Ryota; Fujiwara, Yuki; Uwagawa, Tadashi; Ohashi, Toya; Yanaga, Katsuhiko

Pomalidomide promotes chemosensitization of pancreatic cancer by inhibition of NF-κB

泊马度胺通过抑制NF-κB促进胰腺癌的化疗敏感性。

Shirai, Yoshihiro; Saito, Nobuhiro; Uwagawa, Tadashi; Shiba, Hiroaki; Horiuchi, Takashi; Iwase, Ryota; Haruki, Koichiro; Ohashi, Toya; Yanaga, Katsuhiko