The patient experience of CHAPLE disease: results from interviews conducted as part of a clinical trial for an ultra-rare condition
CHAPLE 病患者体验:一项针对罕见病临床试验的访谈结果
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-024-03436-y
Litcher-Kelly, Leighann; Ozen, Ahmet; Ollis, Sarah; Feldman, Hagit Baris; Yaworsky, Andrew; Medrano, Paolo; Chongsrisawat, Voranush; Perlee, Lorah; Walker, Marisa; Pradeep, Sharanya; Turner-Bowker, Diane M; Kurolap, Alina; Adiv, Orly Eshach; Lenardo, Michael J; Harari, Olivier A; Jalbert, Jessica J