日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CNM-Au8 in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial

CNM-Au8 在肌萎缩侧索硬化症中的应用:HEALEY ALS 平台试验

Berry, James D; Maragakis, Nicholas J; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joseph; McGlothlin, Anna; Stommel, Elijah W; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alex; Shefner, Jeremy; Hall, Meghan; Kittle, Gale; Babu, Suma; Andrews, Jinsy; D'Agostino, Derek; Tustison, Eric; Scirocco, Erica; Giacomelli, Elisa; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Ajroud-Driss, Senda; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin J; Simmons, Zachary; Miller, Timothy; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo Jr; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney E; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Rynders, Austin; Evan, Jacob; Evan, Jeremy; Hartford, Alan; Sepassi, Marjan; Ho, Karen S; Glanzman, Robert; Greenberg, Benjamin; Hotchkin, Michael T; Paganoni, Sabrina; Cudkowicz, Merit E

Pridopidine in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial

普利多吡啶治疗肌萎缩侧索硬化症:HEALEY ALS平台试验

Shefner, Jeremy M; Oskarsson, Björn; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joe; McGlothlin, Anna; Heiman-Patterson, Terry; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alexander V; Hall, Meghan; Kittle, Gale; Berry, James D; Babu, Suma; Andrews, Jinsy; D'Agostino, Derek; Tustison, Eric; Scirocco, Erica; Giacomelli, Elisa; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Ajroud-Driss, Senda; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Miller, Timothy M; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Ladha, Shafeeq; Caress, James B; Swenson, Andrea; Peltier, Amanda; Lewis, Richard A; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Leitner, Melanie L; Chen, Kelly; Goldberg, Y Paul; Cohen, Yael; Geva, Michal; Hayden, Michael R; Paganoni, Sabrina; Cudkowicz, Merit E

Verdiperstat in Amyotrophic Lateral Sclerosis: Results From the Randomized HEALEY ALS Platform Trial

Verdiperstat治疗肌萎缩侧索硬化症:来自随机HEALEY ALS平台试验的结果

Andrews, Jinsy; Paganoni, Sabrina; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joseph; McGlothlin, Anna; Young, Eufrosina; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney; Yu, Hong; Sherman, Alex; Shefner, Jeremy; Hall, Meghan; Kittle, Gale; Connolly, Mariah R; Berry, James D; D'Agostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Heitzman, Daragh; Ajroud-Driss, Senda; Appel, Stanley H; Shroff, Sheetal; Katz, Jonathan; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Goutman, Stephen A; Olney, Nicholas; Miller, Timothy; Fernandes, Joseph Americo; Ilieva, Hristelina; Jawdat, Omar; Weiss, Michael D; Foster, Laura; Vu, Tuan; Ladha, Shafeeq; Owegi, Margaret Ayo; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Swenson, Andrea; Heiman-Patterson, Terry; Caress, James; Fee, Dominic; Peltier, Amanda; Lewis, Richard; Rosenfeld, Jeffrey; Walk, David; Johnson, Kristin; Elliott, Matthew; Kasarskis, Edward J; Rutkove, Seward; McIlduff, Courtney E; Bedlack, Richard; Elman, Lauren; Goyal, Namita A; Rezania, Kourosh; Twydell, Paul; Benatar, Michael; Glass, Jonathan; Cohen, Jeffrey A; Jones, Vovanti; Zilliox, Lindsay; Wymer, James P; Beydoun, Said R; Shah, Jaimin; Pattee, Gary L; Martinez-Thompson, Jennifer; Nayar, Shakti; Granit, Volkan; Donohue, Mary; Grossman, Katheryn; Campbell, Daniel J; Qureshi, Irfan A; Cudkowicz, Merit E; Babu, Suma

Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis: A Randomized Clinical Trial

Zilucoplan治疗肌萎缩侧索硬化症的疗效和安全性:一项随机临床试验

Paganoni, Sabrina; Fournier, Christina N; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joe; McGlothlin, Anna; Ajroud-Driss, Senda; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alexander V; Shefner, Jeremy M; Hall, Meghan; Kittle, Gale; Berry, James D; Babu, Suma; Andrews, Jinsy; Dagostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Miller, Timothy M; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James B; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Harvey, Brittany; Patel, Shital; Mahoney, Paul; Duda, Petra W; Cudkowicz, Merit E

Facilitators and challenges in the implementation of the Care Ecosystem at six clinical sites in the United States: A qualitative study

美国六个临床中心实施护理生态系统的促进因素和挑战:一项定性研究

Sideman, Alissa B; Merrilees, Jennifer; Dulaney, Sarah; Allawala, Mahnoor; Barclay, Michelle; Rosenbloom, Michael; Hanson, Leah R; Ward, Katherine T; Hess, Mailee; Olney, Nicholas T; Lum, Hillary D; Sawyer, R John; Possin, Katherine L

Safety and tolerability of tegoprubart in patients with amyotrophic lateral sclerosis: A Phase 2A clinical trial.

替戈普鲁巴特治疗肌萎缩侧索硬化症患者的安全性和耐受性:一项 2A 期临床试验

Perrin Steven, Ladha Shafeeq, Maragakis Nicholas, Rivner Michael H, Katz Jonathan, Genge Angela, Olney Nicholas, Lange Dale, Heitzman Daragh, Bodkin Cynthia, Jawdat Omar, Goyal Namita A, Bornstein Jeffrey D, Mak Carmen, Appel Stanley H, Paganoni Sabrina

Association of Cognitive and Behavioral Features Between Adults With Tuberous Sclerosis and Frontotemporal Dementia

结节性硬化症和额颞叶痴呆成人患者的认知和行为特征关联

Liu, Andy J; Staffaroni, Adam M; Rojas-Martinez, Julio C; Olney, Nicholas T; Alquezar-Burillo, Carolina; Ljubenkov, Peter A; La Joie, Renaud; Fong, Jamie C; Taylor, Joanne; Karydas, Anna; Ramos, Eliana Marisa; Coppola, Giovanni; Boxer, Adam L; Rabinovici, Gil D; Miller, Bruce L; Kao, Aimee W

Clinical and volumetric changes with increasing functional impairment in familial frontotemporal lobar degeneration

家族性额颞叶变性患者随着功能障碍加重,会出现临床和体积变化

Olney, Nicholas T; Ong, Elise; Goh, Sheng-Yang M; Bajorek, Lynn; Dever, Reilly; Staffaroni, Adam M; Cobigo, Yann; Bock, Meredith; Chiang, Kevin; Ljubenkov, Peter; Kornak, John; Heuer, Hilary W; Wang, Ping; Rascovsky, Katya; Wolf, Amelia; Appleby, Brian; Bove, Jessica; Bordelon, Yvette; Brannelly, Patrick; Brushaber, Danielle; Caso, Christine; Coppola, Giovanni; Dickerson, Bradford C; Dickinson, Susan; Domoto-Reilly, Kimiko; Faber, Kelly; Ferrall, Jessica; Fields, Julie; Fishman, Ann; Fong, Jamie; Foroud, Tatiana; Forsberg, Leah K; Gearhart, Debra J; Ghazanfari, Behnaz; Ghoshal, Nupur; Goldman, Jill; Graff-Radford, Jonathan; Graff-Radford, Neill R; Grant, Ian; Grossman, Murray; Haley, Dana; Hsiung, Gingyuek; Huey, Edward D; Irwin, David J; Jones, David T; Kantarci, Kejal; Karydas, Anna M; Kaufer, Daniel; Kerwin, Diana; Knopman, David S; Kramer, Joel H; Kraft, Ruth; Kremers, Walter; Kukull, Walter; Lapid, Maria I; Litvan, Irene; Mackenzie, Ian R; Maldonado, Miranda; Manoochehri, Masood; McGinnis, Scott M; McKinley, Emily C; Mendez, Mario F; Miller, Bruce L; Onyike, Chiadi; Pantelyat, Alex; Pearlman, Rodney; Petrucelli, Len; Potter, Madeleine; Rademakers, Rosa; Ramos, Eliana M; Rankin, Katherine P; Roberson, Erik D; Rogalski, Emily; Sengdy, Pheth; Shaw, Leslie M; Syrjanen, Jeremy; Tartaglia, M Carmela; Tatton, Nadine; Taylor, Joanne; Toga, Arthur; Trojanowski, John Q; Weintraub, Sandra; Wong, Bonnie; Wszolek, Zbigniew; Boxer, Adam L; Boeve, Brad F; Rosen, Howard J

Clinical value of cerebrospinal fluid neurofilament light chain in semantic dementia

脑脊液神经丝轻链在语义性痴呆中的临床价值

Meeter, Lieke H H; Steketee, Rebecca M E; Salkovic, Dina; Vos, Maartje E; Grossman, Murray; McMillan, Corey T; Irwin, David J; Boxer, Adam L; Rojas, Julio C; Olney, Nicholas T; Karydas, Anna; Miller, Bruce L; Pijnenburg, Yolande A L; Barkhof, Frederik; Sánchez-Valle, Raquel; Lladó, Albert; Borrego-Ecija, Sergi; Diehl-Schmid, Janine; Grimmer, Timo; Goldhardt, Oliver; Santillo, Alexander F; Hansson, Oskar; Vestberg, Susanne; Borroni, Barbara; Padovani, Alessandro; Galimberti, Daniela; Scarpini, Elio; Rohrer, Jonathan D; Woollacott, Ione O C; Synofzik, Matthis; Wilke, Carlo; de Mendonca, Alexandre; Vandenberghe, Rik; Benussi, Luisa; Ghidoni, Roberta; Binetti, Giuliano; Niessen, Wiro J; Papma, Janne M; Seelaar, Harro; Jiskoot, Lize C; de Jong, Frank Jan; Donker Kaat, Laura; Del Campo, Marta; Teunissen, Charlotte E; Bron, Esther E; Van den Berg, Esther; Van Swieten, John C

Primary progressive aphasia and the FTD-MND spectrum disorders: clinical, pathological, and neuroimaging correlates

原发性进行性失语症和额颞叶痴呆-运动神经元病谱系障碍:临床、病理和神经影像学相关性

Vinceti, Giulia; Olney, Nicholas; Mandelli, Maria Luisa; Spina, Salvatore; Hubbard, H Isabel; Santos-Santos, Miguel A; Watson, Christa; Miller, Zachary A; Lomen-Hoerth, Catherine; Nichelli, Paolo; Miller, Bruce L; Grinberg, Lea T; Seeley, William W; Gorno-Tempini, Maria Luisa