Variation of VP2 stoichiometry and deamidation of VP1 during production and their impacts on the transduction efficiency of AAV vectors
生产过程中VP2化学计量比的变化和VP1脱酰胺作用及其对AAV载体转导效率的影响
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101581
Maruno, Takahiro; Fukuhara, Mitsuko; Tsunaka, Yasuo; Matsushita, Aoba; Hirohata, Kiichi; Bandoh, Karin; Onaka, Megumi; Shibuya, Risa; Yamaguchi, Yuki; Nishiumi, Haruka; Nagashima, Yoshiki; Higo, Daisuke; Kuwahara, Toshie; Ueno, Tomoko; Maeda, Masaharu; Kanai-Bai, Guirong; Yamano-Adachi, Noriko; Torisu, Tetsuo; Omasa, Takeshi; Uchiyama, Susumu