End points for sickle cell disease clinical trials: renal and cardiopulmonary, cure, and low-resource settings
镰状细胞病临床试验的终点:肾脏和心肺功能、治愈率以及低资源环境
期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2019000883
Farrell, Ann T; Panepinto, Julie; Desai, Ankit A; Kassim, Adetola A; Lebensburger, Jeffrey; Walters, Mark C; Bauer, Daniel E; Blaylark, Rae M; DiMichele, Donna M; Gladwin, Mark T; Green, Nancy S; Hassell, Kathryn; Kato, Gregory J; Klings, Elizabeth S; Kohn, Donald B; Krishnamurti, Lakshmanan; Little, Jane; Makani, Julie; Malik, Punam; McGann, Patrick T; Minniti, Caterina; Morris, Claudia R; Odame, Isaac; Oneal, Patricia Ann; Setse, Rosanna; Sharma, Poornima; Shenoy, Shalini