Spliceosome mutations are common in persons with myeloproliferative neoplasm-associated myelofibrosis with RBC-transfusion-dependence and correlate with response to pomalidomide
剪接体突变在伴有红细胞输注依赖的骨髓增生性肿瘤相关骨髓纤维化患者中很常见,并且与泊马度胺的疗效相关。
期刊:Leukemia
影响因子:13.4
doi:10.1038/s41375-020-0979-6
Chowdhury, Onima; O'Sullivan, Jennifer; Barkas, Nikolaos; Wang, Guanlin; Buck, Gemma; Hamblin, Angela; Tefferi, Ayalew; Al-Ali, Haifa K; Barosi, Giovanni; Devos, Timothy; Gisslinger, Heinz; Jiang, Qian; Kiladjian, Jean-Jacques; Mesa, Ruben; Passamonti, Francesco; Ribrag, Vincent; Schiller, Gary; Vannucchi, Alessandro M; Zhou, Daobin; McMullin, Mary Frances; Zhong, Jianhua; Gale, Robert Peter; Mead, Adam J