First-in-human autologous implantation of genetically modified adipocytes expressing LCAT for the treatment of familial LCAT deficiency
首次在人体内进行自体移植，将表达LCAT的基因修饰脂肪细胞移植到患者体内，用于治疗家族性LCAT缺乏症。
期刊:Heliyon
影响因子:3.4
doi:10.1016/j.heliyon.2022.e11271
Masayuki Aso ,Tokuo T Yamamoto ,Masayuki Kuroda ,Jun Wada ,Yoshitaka Kubota ,Ko Ishikawa ,Yoshiro Maezawa ,Naoya Teramoto ,Ayako Tawada ,Sakiyo Asada ,Yasuyuki Aoyagi ,Mika Kirinashizawa ,Akinobu Onitake ,Yuta Matsuura ,Kunio Yasunaga ,Shun-Ichi Konno ,Katsuaki Nishino ,Misato Yamamoto ,Junko Miyoshi ,Norihiko Kobayashi ,Masami Tanio ,Takayuki Ikeuchi ,Hidetoshi Igari ,Nobuyuki Mitsukawa ,Hideki Hanaoka ,Koutaro Yokote ,Yasushi Saito
