Efficacy and safety of thalidomide for the treatment of severe recurrent epistaxis in hereditary haemorrhagic telangiectasia: results of a non-randomised, single-centre, phase 2 study
沙利度胺治疗遗传性出血性毛细血管扩张症引起的严重复发性鼻出血的疗效和安全性:一项非随机、单中心、II期研究的结果
期刊:Lancet Haematology
影响因子:17.7
doi:10.1016/S2352-3026(15)00195-7
Invernizzi, Rosangela; Quaglia, Federica; Klersy, Catherine; Pagella, Fabio; Ornati, Federica; Chu, Francesco; Matti, Elina; Spinozzi, Giuseppe; Plumitallo, Sara; Grignani, Pierangela; Olivieri, Carla; Bastia, Raffaella; Bellistri, Francesca; Danesino, Cesare; Benazzo, Marco; Balduini, Carlo L