Germline CRISPR/Cas9-Mediated Gene Editing Prevents Vision Loss in a Novel Mouse Model of Aniridia
种系 CRISPR/Cas9 介导的基因编辑可防止新型无虹膜小鼠模型出现视力丧失
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2020.03.002
Seyedeh Zeinab Mirjalili Mohanna, Jack W Hickmott, Siu Ling Lam, Nina Y Chiu, Tess C Lengyell, Beatrice M Tam, Orson L Moritz, Elizabeth M Simpson