日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Genotype, oxidase status, and preceding infection or autoinflammation do not affect allogeneic HCT outcomes for CGD

基因型、氧化酶状态以及既往感染或自身炎症均不影响慢性肉芽肿病(CGD)患者的异基因造血干细胞移植(HCT)预后。

Leiding, Jennifer W; Arnold, Danielle E; Parikh, Suhag; Logan, Brent; Marsh, Rebecca A; Griffith, Linda M; Wu, Ruizhe; Kidd, Sharon; Mallhi, Kanwaldeep; Chellapandian, Deepak; Si Lim, Stephanie J; Grunebaum, Eyal; Falcone, E Liana; Murguia-Favela, Luis; Grossman, Debbi; Prasad, Vinod K; Heimall, Jennifer R; Touzot, Fabien; Burroughs, Lauri M; Bleesing, Jack; Kapoor, Neena; Dara, Jasmeen; Williams, Olatundun; Kapadia, Malika; Oshrine, Benjamin R; Bednarski, Jeffrey J; Rayes, Ahmad; Chong, Hey; Cuvelier, Geoffrey D E; Forbes Satter, Lisa R; Martinez, Caridad; Vander Lugt, Mark T; Yu, Lolie C; Chandrakasan, Shanmuganathan; Joshi, Avni; Prockop, Susan E; Dávila Saldaña, Blachy J; Aquino, Victor; Broglie, Larisa A; Ebens, Christen L; Madden, Lisa M; DeSantes, Kenneth; Milner, Jordan; Rangarajan, Hemalatha G; Shah, Ami J; Gillio, Alfred P; Knutsen, Alan P; Miller, Holly K; Moore, Theodore B; Graham, Pamela; Bauchat, Andrea; Bunin, Nancy J; Teira, Pierre; Petrovic, Aleksandra; Chandra, Sharat; Abdel-Azim, Hisham; Dorsey, Morna J; Birbrayer, Olga; Cowan, Morton J; Dvorak, Christopher C; Haddad, Elie; Kohn, Donald B; Notarangelo, Luigi D; Pai, Sung-Yun; Puck, Jennifer M; Pulsipher, Michael A; Torgerson, Troy R; Malech, Harry L; Kang, Elizabeth M

A diagnostic classifier for pediatric chronic graft-versus-host disease: results of the ABLE/PBMTC 1202 study

儿童慢性移植物抗宿主病诊断分类器:ABLE/PBMTC 1202 研究结果

Cuvelier, Geoffrey D E; Ng, Bernard; Abdossamadi, Sayeh; Nemecek, Eneida R; Melton, Alexis; Kitko, Carrie L; Lewis, Victor A; Schechter, Tal; Jacobsohn, David A; Harris, Andrew C; Pulsipher, Michael A; Bittencourt, Henrique; Choi, Sung Won; Caywood, Emi H; Kasow, Kimberly A; Bhatia, Monica; Oshrine, Benjamin R; Chaudhury, Sonali; Coulter, Donald; Chewning, Joseph H; Joyce, Michael; Savaşan, Süreyya; Pawlowska, Anna B; Megason, Gail C; Mitchell, David; Cheerva, Alexandra C; Lawitschka, Anita; Ostroumov, Elena; Schultz, Kirk R

Molecular and phenotypic diversity of CBL-mutated juvenile myelomonocytic leukemia

CBL突变型幼年骨髓单核细胞白血病的分子和表型多样性

Hecht, Anna; Meyer, Julia A; Behnert, Astrid; Wong, Eric; Chehab, Farid; Olshen, Adam; Hechmer, Aaron; Aftandilian, Catherine; Bhat, Rukhmi; Choi, Sung Won; Chonat, Satheesh; Farrar, Jason E; Fluchel, Mark; Frangoul, Haydar; Han, Jennifer H; Kolb, Edward A; Kuo, Dennis J; MacMillan, Margaret L; Maese, Luke; Maloney, Kelly W; Narendran, Aru; Oshrine, Benjamin; Schultz, Kirk R; Sulis, Maria L; Van Mater, David; Tasian, Sarah K; Hofmann, Wolf-Karsten; Loh, Mignon L; Stieglitz, Elliot

Acute Left Ventricular Dysfunction Following Gemtuzumab Ozogamicin in Two Pediatric AML Patients

两例儿童急性髓系白血病患者接受吉妥珠单抗治疗后出现急性左心室功能障碍

McNerney, Kevin O; Oranges, Katelyn; Seif, Alix E; Oshrine, Benjamin; Ky, Bonnie; Lin, Kimberly Y; Getz, Kelly D; Aplenc, Richard

Survival Benefit for Individuals With Constitutional Mismatch Repair Deficiency Undergoing Surveillance

接受监测的先天性错配修复缺陷患者的生存获益

Durno, Carol; Ercan, Ayse Bahar; Bianchi, Vanessa; Edwards, Melissa; Aronson, Melyssa; Galati, Melissa; Atenafu, Eshetu G; Abebe-Campino, Gadi; Al-Battashi, Abeer; Alharbi, Musa; Azad, Vahid Fallah; Baris, Hagit N; Basel, Donald; Bedgood, Raymond; Bendel, Anne; Ben-Shachar, Shay; Blumenthal, Deborah T; Blundell, Maude; Bornhorst, Miriam; Bronsema, Annika; Cairney, Elizabeth; Rhode, Sara; Caspi, Shani; Chamdin, Aghiad; Chiaravalli, Stefano; Constantini, Shlomi; Crooks, Bruce; Das, Anirban; Dvir, Rina; Farah, Roula; Foulkes, William D; Frenkel, Zehavit; Gallinger, Bailey; Gardner, Sharon; Gass, David; Ghalibafian, Mithra; Gilpin, Catherine; Goldberg, Yael; Goudie, Catherine; Hamid, Syed Ahmer; Hampel, Heather; Hansford, Jordan R; Harlos, Craig; Hijiya, Nobuko; Hsu, Saunders; Kamihara, Junne; Kebudi, Rejin; Knipstein, Jeffrey; Koschmann, Carl; Kratz, Christian; Larouche, Valerie; Lassaletta, Alvaro; Lindhorst, Scott; Ling, Simon C; Link, Michael P; Loret De Mola, Rebecca; Luiten, Rebecca; Lurye, Michal; Maciaszek, Jamie L; MagimairajanIssai, Vanan; Maher, Ossama M; Massimino, Maura; McGee, Rose B; Mushtaq, Naureen; Mason, Gary; Newmark, Monica; Nicholas, Garth; Nichols, Kim E; Nicolaides, Theodore; Opocher, Enrico; Osborn, Michael; Oshrine, Benjamin; Pearlman, Rachel; Pettee, Daniel; Rapp, Jan; Rashid, Mohsin; Reddy, Alyssa; Reichman, Lara; Remke, Marc; Robbins, Gabriel; Roy, Sumita; Sabel, Magnus; Samuel, David; Scheers, Isabelle; Schneider, Kami Wolfe; Sen, Santanu; Stearns, Duncan; Sumerauer, David; Swallow, Carol; Taylor, Leslie; Thomas, Gregory; Toledano, Helen; Tomboc, Patrick; Van Damme, An; Winer, Ira; Yalon, Michal; Yen, Lee Yi; Zapotocky, Michal; Zelcer, Shayna; Ziegler, David S; Zimmermann, Stefanie; Hawkins, Cynthia; Malkin, David; Bouffet, Eric; Villani, Anita; Tabori, Uri

Infections in Infants with SCID: Isolation, Infection Screening, and Prophylaxis in PIDTC Centers

重症联合免疫缺陷症婴儿的感染:PIDTC中心的隔离、感染筛查和预防

Dorsey, Morna J; Wright, Nicola A M; Chaimowitz, Natalia S; Dávila Saldaña, Blachy J; Miller, Holly; Keller, Michael D; Thakar, Monica S; Shah, Ami J; Abu-Arja, Rolla; Andolina, Jeffrey; Aquino, Victor; Barnum, J L; Bednarski, Jeffrey J; Bhatia, Monica; Bonilla, Francisco A; Butte, Manish J; Bunin, Nancy J; Chandra, Sharat; Chaudhury, Sonali; Chen, Karin; Chong, Hey; Cuvelier, Geoffrey D E; Dalal, Jignesh; DeFelice, Magee L; DeSantes, Kenneth B; Forbes, Lisa R; Gillio, Alfred; Goldman, Fred; Joshi, Avni Y; Kapoor, Neena; Knutsen, Alan P; Kobrynski, Lisa; Lieberman, Jay A; Leiding, Jennifer W; Oshrine, Benjamin; Patel, Kiran P; Prockop, Susan; Quigg, Troy C; Quinones, Ralph; Schultz, Kirk R; Seroogy, Christine; Shyr, David; Siegel, Subhadra; Smith, Angela R; Torgerson, Troy R; Vander Lugt, Mark T; Yu, Lolie C; Cowan, Morton J; Buckley, Rebecca H; Dvorak, Christopher C; Griffith, Linda M; Haddad, Elie; Kohn, Donald B; Logan, Brent; Notarangelo, Luigi D; Pai, Sung-Yun; Puck, Jennifer; Pulsipher, Michael A; Heimall, Jennifer

Effectiveness and Complication Rate of Percutaneous Endoscopic Gastrostomy Placement in Pediatric Oncology Patients

经皮内镜胃造瘘术在儿童肿瘤患者中的有效性和并发症发生率

Kidder, Molly; Phen, Claudia; Brown, Jerry; Kimsey, Kathryn; Oshrine, Benjamin; Ghazarian, Sharon; Mateus, Jazmine; Amankwah, Ernest; Wilsey, Michael

Hematopoietic Cell Transplantation in Patients With Primary Immune Regulatory Disorders (PIRD): A Primary Immune Deficiency Treatment Consortium (PIDTC) Survey

原发性免疫调节障碍(PIRD)患者的造血干细胞移植:原发性免疫缺陷治疗联盟(PIDTC)调查

Chan, Alice Y; Leiding, Jennifer W; Liu, Xuerong; Logan, Brent R; Burroughs, Lauri M; Allenspach, Eric J; Skoda-Smith, Suzanne; Uzel, Gulbu; Notarangelo, Luigi D; Slatter, Mary; Gennery, Andrew R; Smith, Angela R; Pai, Sung-Yun; Jordan, Michael B; Marsh, Rebecca A; Cowan, Morton J; Dvorak, Christopher C; Craddock, John A; Prockop, Susan E; Chandrakasan, Shanmuganathan; Kapoor, Neena; Buckley, Rebecca H; Parikh, Suhag; Chellapandian, Deepak; Oshrine, Benjamin R; Bednarski, Jeffrey J; Cooper, Megan A; Shenoy, Shalini; Davila Saldana, Blachy J; Forbes, Lisa R; Martinez, Caridad; Haddad, Elie; Shyr, David C; Chen, Karin; Sullivan, Kathleen E; Heimall, Jennifer; Wright, Nicola; Bhatia, Monica; Cuvelier, Geoffrey D E; Goldman, Frederick D; Meyts, Isabelle; Miller, Holly K; Seidel, Markus G; Vander Lugt, Mark T; Bacchetta, Rosa; Weinacht, Katja G; Andolina, Jeffrey R; Caywood, Emi; Chong, Hey; de la Morena, Maria Teresa; Aquino, Victor M; Shereck, Evan; Walter, Jolan E; Dorsey, Morna J; Seroogy, Christine M; Griffith, Linda M; Kohn, Donald B; Puck, Jennifer M; Pulsipher, Michael A; Torgerson, Troy R

Correction: Chronic Granulomatous Disease-Associated IBD Resolves and Does Not Adversely Impact Survival Following Allogeneic HCT

更正:慢性肉芽肿病相关炎症性肠病可消退,且不会对异基因造血干细胞移植后的生存率产生不利影响。

Marsh, Rebecca A; Leiding, Jennifer W; Logan, Brent R; Griffith, Linda M; Arnold, Danielle E; Haddad, Elie; Falcone, E Liana; Yin, Ziyan; Patel, Kadam; Arbuckle, Erin; Bleesing, Jack J; Sullivan, Kathleen E; Heimall, Jennifer; Burroughs, Lauri M; Skoda-Smith, Suzanne; Chandrakasan, Shanmuganathan; Yu, Lolie C; Oshrine, Benjamin R; Cuvelier, Geoffrey D E; Thakar, Monica S; Chen, Karin; Teira, Pierre; Shenoy, Shalini; Phelan, Rachel; Forbes, Lisa R; Martinez, Caridad; Chellapandian, Deepak; Dávila Saldaña, Blachy J; Shah, Ami J; Weinacht, Katja G; Joshi, Avni; Boulad, Farid; Quigg, Troy C; Dvorak, Christopher C; Grossman, Debi; Torgerson, Troy; Graham, Pamela; Prasad, Vinod; Knutsen, Alan; Chong, Hey; Miller, Holly; de la Morena, M Teresa; DeSantes, Kenneth; Cowan, Morton J; Notarangelo, Luigi D; Kohn, Donald B; Stenger, Elizabeth; Pai, Sung-Yun; Routes, John M; Puck, Jennifer M; Kapoor, Neena; Pulsipher, Michael A; Malech, Harry L; Parikh, Suhag; Kang, Elizabeth M

RARE-17. SURVIVAL BENEFIT FOR INDIVIDUALS WITH CONSTITUTIONAL MISMATCH REPAIR DEFICIENCY SYNDROME AND BRAIN TUMORS WHO UNDERGO SURVEILLANCE PROTOCOL. A REPORT FROM THE INTERNATIONAL REPLICATION REPAIR CONSORTIUM

罕见-17. 接受监测方案的先天性错配修复缺陷综合征合并脑肿瘤患者的生存获益。国际复制修复联盟报告

Mehrian-Shai, Ruty; Ercan, Ayse Bahar; Durno, Carol; Bianchi, Vanessa J; Edwards, Melissa; Aronson, Melyssa; Bouffet, Eric; Al-Battashi, Abeer; Alharbi, Musa; Basel, Donald; Bedgood, Raymond; Bendel, Anne; Blumenthal, Deborah T; Bornhorst, Miriam; Bronsema, Annika; Cairney, Elizabeth; Carroll, Sara; Chamdin, Aghiad; Chiaravalli, Stefano; Constantini, Shlomi; Das, Anirban; Dvir, Rina; Farah, Roula; Foulkes, William; Frenkel, Zehavit; Gardner, Sharon; Ghalibafian, Mithra; Gilpin, Cathy; Goudie, Catherine; Hamid, Syed Ahmer; Hansford, Jordan; Harlos, Craig; Hijiya, Nobuko; Hsu, Saunders; Kamihara, Junne; Knipstein, Jeffrey; Koschmann, Carl; Larouche, Valerie; Lassaletta, Alvaro; Lindhorst, Scott; Ling, Simon; Link, Michael; De Mola, Rebecca Loret; Luiten, Rebecca; Lurye, Michal; Maciaszek, Jamie; Magimairajan, Vanan; Maher, Ossama; Massimino, Maura; Mushtaq, Naureen; Newmark, Monica; Nicholas, Garth; Nichols, Kim; Nicolaides, Theodore; Opocher, Enrico; Osborn, Michael; Oshrine, Benjamin; Pearlman, Rachel; Pettee, Daniel; Rapp, Jan; Rashid, Mohsin; Reddy, Alyssa; Reichman, Lara; Remke, Marc; Robbins, Gabriel; Sabel, Magnus; Samuel, David; Scheers, Isabelle; Sen, Santanu; Stearns, Duncan; Sumerauer, David; Swallow, Carol; Taylor, Leslie; Toledano, Helen; Tomboc, Patrick; Van Damme, An; Winer, Ira; Yalon, Michal; Yen, Lee Yi; Zapotocky, Michal; Azad, Vahid Fallah; Zelcer, Shayna; Ziegler, David; Zimmerman, Stefanie; Tabori, Uri