Innate immune response to AAV-based gene therapy vectors: Mechanisms of complement activation and cytokine release
针对基于腺相关病毒(AAV)基因治疗载体的先天免疫反应:补体激活和细胞因子释放机制
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101551
Xicluna, Rebecca; Schwalie, Petra C; Bell, Emma; Von Tell, Desiree; Steiner, Guido; Seeger, Emily; Freen-van Heeren, Julian J; Turksma, Annelies W; Pouw, Richard B; Schwandt, Timo; Otteneder, Michael B; Rispens, Theo; Brouwer, Mieke C; Bertinetti-Lapatki, Cristina; Haegel, Hélène