Direct delivery of Cas9 or base editor protein and guide RNA complex enables genome editing in the retina
将Cas9或碱基编辑器蛋白与引导RNA复合物直接递送至视网膜,即可实现视网膜基因组编辑。
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2024.102349.
Juliette Pulman ,Catherine Botto ,Hugo Malki ,Duohao Ren ,Paul Oudin ,Anne De Cian ,Marie As ,Charlotte Izabelle ,Bruno Saubamea ,Valerie Forster ,Stéphane Fouquet ,Camille Robert ,Céline Portal ,Aziz El-Amraoui ,Sylvain Fisson ,Jean-Paul Concordet ,Deniz Dalkara