日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CNM-Au8 in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial

CNM-Au8 在肌萎缩侧索硬化症中的应用:HEALEY ALS 平台试验

Berry, James D; Maragakis, Nicholas J; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joseph; McGlothlin, Anna; Stommel, Elijah W; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alex; Shefner, Jeremy; Hall, Meghan; Kittle, Gale; Babu, Suma; Andrews, Jinsy; D'Agostino, Derek; Tustison, Eric; Scirocco, Erica; Giacomelli, Elisa; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Ajroud-Driss, Senda; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin J; Simmons, Zachary; Miller, Timothy; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo Jr; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney E; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Rynders, Austin; Evan, Jacob; Evan, Jeremy; Hartford, Alan; Sepassi, Marjan; Ho, Karen S; Glanzman, Robert; Greenberg, Benjamin; Hotchkin, Michael T; Paganoni, Sabrina; Cudkowicz, Merit E

Pridopidine in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial

普利多吡啶治疗肌萎缩侧索硬化症:HEALEY ALS平台试验

Shefner, Jeremy M; Oskarsson, Björn; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joe; McGlothlin, Anna; Heiman-Patterson, Terry; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alexander V; Hall, Meghan; Kittle, Gale; Berry, James D; Babu, Suma; Andrews, Jinsy; D'Agostino, Derek; Tustison, Eric; Scirocco, Erica; Giacomelli, Elisa; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Ajroud-Driss, Senda; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Miller, Timothy M; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Ladha, Shafeeq; Caress, James B; Swenson, Andrea; Peltier, Amanda; Lewis, Richard A; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Leitner, Melanie L; Chen, Kelly; Goldberg, Y Paul; Cohen, Yael; Geva, Michal; Hayden, Michael R; Paganoni, Sabrina; Cudkowicz, Merit E

Verdiperstat in Amyotrophic Lateral Sclerosis: Results From the Randomized HEALEY ALS Platform Trial

Verdiperstat治疗肌萎缩侧索硬化症:来自随机HEALEY ALS平台试验的结果

Andrews, Jinsy; Paganoni, Sabrina; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joseph; McGlothlin, Anna; Young, Eufrosina; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney; Yu, Hong; Sherman, Alex; Shefner, Jeremy; Hall, Meghan; Kittle, Gale; Connolly, Mariah R; Berry, James D; D'Agostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Heitzman, Daragh; Ajroud-Driss, Senda; Appel, Stanley H; Shroff, Sheetal; Katz, Jonathan; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Goutman, Stephen A; Olney, Nicholas; Miller, Timothy; Fernandes, Joseph Americo; Ilieva, Hristelina; Jawdat, Omar; Weiss, Michael D; Foster, Laura; Vu, Tuan; Ladha, Shafeeq; Owegi, Margaret Ayo; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Swenson, Andrea; Heiman-Patterson, Terry; Caress, James; Fee, Dominic; Peltier, Amanda; Lewis, Richard; Rosenfeld, Jeffrey; Walk, David; Johnson, Kristin; Elliott, Matthew; Kasarskis, Edward J; Rutkove, Seward; McIlduff, Courtney E; Bedlack, Richard; Elman, Lauren; Goyal, Namita A; Rezania, Kourosh; Twydell, Paul; Benatar, Michael; Glass, Jonathan; Cohen, Jeffrey A; Jones, Vovanti; Zilliox, Lindsay; Wymer, James P; Beydoun, Said R; Shah, Jaimin; Pattee, Gary L; Martinez-Thompson, Jennifer; Nayar, Shakti; Granit, Volkan; Donohue, Mary; Grossman, Katheryn; Campbell, Daniel J; Qureshi, Irfan A; Cudkowicz, Merit E; Babu, Suma

Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis: A Randomized Clinical Trial

Zilucoplan治疗肌萎缩侧索硬化症的疗效和安全性:一项随机临床试验

Paganoni, Sabrina; Fournier, Christina N; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joe; McGlothlin, Anna; Ajroud-Driss, Senda; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alexander V; Shefner, Jeremy M; Hall, Meghan; Kittle, Gale; Berry, James D; Babu, Suma; Andrews, Jinsy; Dagostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Miller, Timothy M; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James B; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Harvey, Brittany; Patel, Shital; Mahoney, Paul; Duda, Petra W; Cudkowicz, Merit E

High prevalence of multi-drug resistant H58 Salmonella Typhi and emerging fluoroquinolone resistance among febrile children in Nairobi County, Kenya

肯尼亚内罗毕县发热儿童中多重耐药性H58型伤寒沙门氏菌高发,且氟喹诺酮类耐药性日益增强

Kavai, Susan Mutile; Mbae, Cecilia; Mugo, Michael; Njoroge, Peter; Chepchirchir, Jessica; Wambui, Naomi; Anyona, Steve; Imoli, Diana; Ng'etich, Ronald; Kibet, Evans; Odityo, Georgina; Mundalo, Sheillah; Wairimu, Celestine; Kariuki, Mary; Njuguna, Amos; Wamucii, Evelyn; Mbithi, Winfred; Owegi, Darius; Muturi, Peter; Kebenei, Collins; Miriti, Humphrey; Komen, Naomi; Kioko, Christine; Kawira, Maureen; Kavai, June; Osman, Rahma; Wakio, Zillah; Ongadi, Beatrice; Onsare, Robert; Kering, Kelvin; Kariuki, Samuel

Effect of sodium phenylbutyrate/taurursodiol on tracheostomy/ventilation-free survival and hospitalisation in amyotrophic lateral sclerosis: long-term results from the CENTAUR trial

苯丁酸钠/牛磺熊去氧胆酸对肌萎缩侧索硬化症患者无气管切开/机械通气生存率和住院率的影响:CENTAUR试验的长期结果

Paganoni, Sabrina; Hendrix, Suzanne; Dickson, Samuel P; Knowlton, Newman; Berry, James D; Elliott, Michael A; Maiser, Samuel; Karam, Chafic; Caress, James B; Owegi, Margaret Ayo; Quick, Adam; Wymer, James; Goutman, Stephen A; Heitzman, Daragh; Heiman-Patterson, Terry D; Jackson, Carlayne; Quinn, Colin; Rothstein, Jeffrey D; Kasarskis, Edward J; Katz, Jonathan; Jenkins, Liberty; Ladha, Shafeeq S; Miller, Timothy M; Scelsa, Stephen N; Vu, Tuan H; Fournier, Christina; Johnson, Kristin M; Swenson, Andrea; Goyal, Namita; Pattee, Gary L; Babu, Suma; Chase, Marianne; Dagostino, Derek; Hall, Meghan; Kittle, Gale; Eydinov, Mathew; Ostrow, Joseph; Pothier, Lindsay; Randall, Rebecca; Shefner, Jeremy M; Sherman, Alexander V; Tustison, Eric; Vigneswaran, Prasha; Yu, Hong; Cohen, Joshua; Klee, Justin; Tanzi, Rudolph; Gilbert, Walter; Yeramian, Patrick; Cudkowicz, Merit

Long-term survival of participants in the CENTAUR trial of sodium phenylbutyrate-taurursodiol in amyotrophic lateral sclerosis

CENTAUR试验中苯丁酸钠-牛磺熊去氧胆酸治疗肌萎缩侧索硬化症患者的长期生存情况

Paganoni, Sabrina; Hendrix, Suzanne; Dickson, Samuel P; Knowlton, Newman; Macklin, Eric A; Berry, James D; Elliott, Michael A; Maiser, Samuel; Karam, Chafic; Caress, James B; Owegi, Margaret Ayo; Quick, Adam; Wymer, James; Goutman, Stephen A; Heitzman, Daragh; Heiman-Patterson, Terry D; Jackson, Carlayne E; Quinn, Colin; Rothstein, Jeffrey D; Kasarskis, Edward J; Katz, Jonathan; Jenkins, Liberty; Ladha, Shafeeq; Miller, Timothy M; Scelsa, Stephen N; Vu, Tuan H; Fournier, Christina N; Glass, Jonathan D; Johnson, Kristin M; Swenson, Andrea; Goyal, Namita A; Pattee, Gary L; Andres, Patricia L; Babu, Suma; Chase, Marianne; Dagostino, Derek; Hall, Meghan; Kittle, Gale; Eydinov, Matthew; McGovern, Michelle; Ostrow, Joseph; Pothier, Lindsay; Randall, Rebecca; Shefner, Jeremy M; Sherman, Alexander V; St Pierre, Maria E; Tustison, Eric; Vigneswaran, Prasha; Walker, Jason; Yu, Hong; Chan, James; Wittes, Janet; Yu, Zi-Fan; Cohen, Joshua; Klee, Justin; Leslie, Kent; Tanzi, Rudolph E; Gilbert, Walter; Yeramian, Patrick D; Schoenfeld, David; Cudkowicz, Merit E

Trial of Sodium Phenylbutyrate-Taurursodiol for Amyotrophic Lateral Sclerosis

苯丁酸钠-牛磺熊去氧胆酸治疗肌萎缩侧索硬化症的试验

Paganoni, Sabrina; Macklin, Eric A; Hendrix, Suzanne; Berry, James D; Elliott, Michael A; Maiser, Samuel; Karam, Chafic; Caress, James B; Owegi, Margaret A; Quick, Adam; Wymer, James; Goutman, Stephen A; Heitzman, Daragh; Heiman-Patterson, Terry; Jackson, Carlayne E; Quinn, Colin; Rothstein, Jeffrey D; Kasarskis, Edward J; Katz, Jonathan; Jenkins, Liberty; Ladha, Shafeeq; Miller, Timothy M; Scelsa, Stephen N; Vu, Tuan H; Fournier, Christina N; Glass, Jonathan D; Johnson, Kristin M; Swenson, Andrea; Goyal, Namita A; Pattee, Gary L; Andres, Patricia L; Babu, Suma; Chase, Marianne; Dagostino, Derek; Dickson, Samuel P; Ellison, Noel; Hall, Meghan; Hendrix, Kent; Kittle, Gale; McGovern, Michelle; Ostrow, Joseph; Pothier, Lindsay; Randall, Rebecca; Shefner, Jeremy M; Sherman, Alexander V; Tustison, Eric; Vigneswaran, Prasha; Walker, Jason; Yu, Hong; Chan, James; Wittes, Janet; Cohen, Joshua; Klee, Justin; Leslie, Kent; Tanzi, Rudolph E; Gilbert, Walter; Yeramian, Patrick D; Schoenfeld, David; Cudkowicz, Merit E

SOD1 Suppression with Adeno-Associated Virus and MicroRNA in Familial ALS

腺相关病毒和microRNA抑制家族性ALS中的SOD1

Mueller, Christian; Berry, James D; McKenna-Yasek, Diane M; Gernoux, Gwladys; Owegi, Margaret A; Pothier, Lindsay M; Douthwright, Catherine L; Gelevski, Dario; Luppino, Sarah D; Blackwood, Meghan; Wightman, Nicholas S; Oakley, Derek H; Frosch, Matthew P; Flotte, Terrence R; Cudkowicz, Merit E; Brown, Robert H Jr

NurOwn, phase 2, randomized, clinical trial in patients with ALS: Safety, clinical, and biomarker results

NurOwn 针对 ALS 患者的 II 期随机临床试验:安全性、临床和生物标志物结果

Berry, James D; Cudkowicz, Merit E; Windebank, Anthony J; Staff, Nathan P; Owegi, Margaret; Nicholson, Katherine; McKenna-Yasek, Diane; Levy, Yossef S; Abramov, Natalie; Kaspi, Haggai; Mehra, Munish; Aricha, Revital; Gothelf, Yael; Brown, Robert H