日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A novel PLpro inhibitor improves outcomes in a pre-clinical model of long COVID.

一种新型PLpro抑制剂改善了新冠肺炎长期症状的临床前模型的结果

M Bader Stefanie, Calleja Dale J, Devine Shane M, Kuchel Nathan W, Lu Bernadine G C, Wu Xinyu, Birkinshaw Richard W, Bhandari Reet, Loi Katie, Volpe Rohan, Khakham Yelena, Au Amanda E, Blackmore Timothy R, Mackiewicz Liana, Dayton Merle, Schaefer Jan, Scherer Lena, Stock Angus T, Cooney James P, Schoffer Kael, Maluenda Ana, Kleeman Elizabeth A, Davidson Kathryn C, Allison Cody C, Ebert Gregor, Chen Gong, Katneni Kasiram, Klemm Theresa A, Nachbur Ueli, Georgy Smitha Rose, Czabotar Peter E, Hannan Anthony J, Putoczki Tracy L, Tanzer Maria, Pellegrini Marc, Lechtenberg Bernhard C, Charman Susan A, Call Melissa J, Mitchell Jeffrey P, Lowes Kym N, Lessene Guillaume, Doerflinger Marcel, Komander David

Gene therapy with bidridistrogene xeboparvovec for limb-girdle muscular dystrophy type 2E/R4: phase 1/2 trial results

使用 bidridistrogene xeboparvovec 进行 2E/R4 型肢带型肌营养不良症基因治疗:1/2 期临床试验结果

Jerry R Mendell, Eric R Pozsgai, Sarah Lewis, Danielle A Griffin, Linda P Lowes, Lindsay N Alfano, Kelly J Lehman, Kathleen Church, Natalie F Reash, Megan A Iammarino, Brenna Sabo, Rachael Potter, Sarah Neuhaus, Xiaoxi Li, Herb Stevenson, Louise R Rodino-Klapac

Increase in Full-Length Dystrophin by Exon Skipping in Duchenne Muscular Dystrophy Patients with Single Exon Duplications: An Open-label Study

杜氏肌营养不良症患者中存在单个外显子重复,外显子跳跃导致全长肌营养不良蛋白增加:一项开放标签研究

Stefan Nicolau, Jyoti Malhotra, Maryann Kaler, Pamela Magistrado-Coxen, Megan A Iammarino, Natalie F Reash, Emma C Frair, Saranga Wijeratne, Benjamin J Kelly, Peter White, Linda P Lowes, Megan A Waldrop, Kevin M Flanigan

Validity of remote live stream video evaluation of the North Star Ambulatory Assessment in patients with Duchenne muscular dystrophy

远程实时视频评估北极星步行评估在杜氏肌营养不良症患者中的有效性

P Lowes, Linda; Alfano, Lindsay N; Iammarino, Megan A; Reash, Natalie F; Giblin, Kathryn; Hu, Larry; Yu, Lixi; Wang, Shufang; Salazar, Rachel; Mendell, Jerry R

Circulating tumor cells detected in follow-up predict survival outcomes in tri-modality management of advanced non-metastatic esophageal cancer: a secondary analysis of the QUINTETT randomized trial

在晚期非转移性食管癌三联疗法治疗中,随访中检测到的循环肿瘤细胞可预测生存结果:QUINTETT随机试验的二次分析

Yu, Edward; Allan, Alison L; Sanatani, Michael; Lewis, Debra; Warner, Andrew; Dar, A Rashid; Yaremko, Brian P; Lowes, Lori E; Palma, David A; Raphael, Jacques; Vincent, Mark D; Rodrigues, George B; Fortin, Dalilah; Inculet, Richard I; Frechette, Eric; Bierer, Joel; Law, Jeffery; Younus, Jawaid; Malthaner, Richard A

Follistatin Gene Therapy for Sporadic Inclusion Body Myositis Improves Functional Outcomes

卵泡抑素基因治疗散发性包涵体肌炎可改善功能结果

Jerry R Mendell, Zarife Sahenk, Samiah Al-Zaidy, Louise R Rodino-Klapac, Linda P Lowes, Lindsay N Alfano, Katherine Berry, Natalie Miller, Mehmet Yalvac, Igor Dvorchik, Melissa Moore-Clingenpeel, Kevin M Flanigan, Kathleen Church, Kim Shontz, Choumpree Curry, Sarah Lewis, Markus McColly, Mark J Hoga

A phase 1/2a follistatin gene therapy trial for becker muscular dystrophy

贝克尔型肌营养不良症的 1/2a 期卵泡抑素基因治疗试验

Jerry R Mendell, Zarife Sahenk, Vinod Malik, Ana M Gomez, Kevin M Flanigan, Linda P Lowes, Lindsay N Alfano, Katherine Berry, Eric Meadows, Sarah Lewis, Lyndsey Braun, Kim Shontz, Maria Rouhana, Kelly Reed Clark, Xiomara Q Rosales, Samiah Al-Zaidy, Alessandra Govoni, Louise R Rodino-Klapac, Mark J H