Antisense oligonucleotide eluforsen improves CFTR function in F508del cystic fibrosis
反义寡核苷酸eluforsen可改善F508del囊性纤维化患者的CFTR功能
期刊:Journal of Cystic Fibrosis
影响因子:6
doi:10.1016/j.jcf.2018.10.015
Sermet-Gaudelus, Isabelle; Clancy, John P; Nichols, David P; Nick, Jerry A; De Boeck, Kris; Solomon, George M; Mall, Marcus A; Bolognese, James; Bouisset, Florilene; den Hollander, Wilhelmina; Paquette-Lamontagne, Nicolas; Tomkinson, Nigel; Henig, Noreen; Elborn, J Stuart; Rowe, Steven M