日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Mobility and Quality of Life in Children with Paediatric-Onset Hypophosphatasia Treated with Asfotase Alfa: Results from UK Managed Access Agreement

阿司匹林α治疗儿童期起病的低磷酸血症患儿的活动能力和生活质量:英国管理准入协议的结果

Padidela, Raja; Bishop, Nick; Arundel, Paul; Fang, Shona; Zygouras, Alexandros; Mughal, M Zulf; Shaw, Nick; Saraff, Vrinda

Burosumab vs conventional therapy in children with X-linked hypophosphatemia: results of the open-label, phase 3 extension period

布罗索单抗与常规疗法治疗X连锁低磷血症患儿:开放标签3期扩展研究结果

Ward, Leanne M; Högler, Wolfgang; Glorieux, Francis H; Portale, Anthony A; Whyte, Michael P; Munns, Craig F; Nilsson, Ola; Simmons, Jill H; Padidela, Raja; Namba, Noriyuki; Cheong, Hae Il; Sochett, Etienne; Muroya, Koji; Tanaka, Hiroyuki; Pitukcheewanont, Pisit; Gottesman, Gary S; Biggin, Andrew; Perwad, Farzana; Chen, Angel; Lawrence Merritt Ii, John; Imel, Erik A

Burosumab vs Phosphate/Active Vitamin D in Pediatric X-Linked Hypophosphatemia: A Subgroup Analysis by Dose Level

布罗索单抗与磷酸盐/活性维生素D治疗儿童X连锁低磷血症:按剂量水平进行的亚组分析

Imel, Erik A; Glorieux, Francis H; Whyte, Michael P; Portale, Anthony A; Munns, Craig F; Nilsson, Ola; Simmons, Jill H; Padidela, Raja; Namba, Noriyuki; Cheong, Hae Il; Pitukcheewanont, Pisit; Sochett, Etienne; Högler, Wolfgang; Muroya, Koji; Tanaka, Hiroyuki; Gottesman, Gary S; Biggin, Andrew; Perwad, Farzana; Chen, Angel; Roberts, Mary Scott; Ward, Leanne M

Refractory Rickets

难治性佝偻病

Chinoy, Amish; Padidela, Raja

Reducing Metabolic Bone Disease Burden in Intestinal Failure Children on Home Parenteral Nutrition

降低接受家庭肠外营养治疗的肠衰竭儿童的代谢性骨病负担

Tridimas, Andreas; Padidela, Raja; Bassett, John; Wood, Rachel; Lawson, Maureen; Fagbemi, Andrew; Morris, Timothy J

Effect of Burosumab Compared With Conventional Therapy on Younger vs Older Children With X-linked Hypophosphatemia

布罗索单抗与常规疗法对X连锁低磷血症患儿(年龄较小和年龄较大)的疗效比较

Ward, Leanne M; Glorieux, Francis H; Whyte, Michael P; Munns, Craig F; Portale, Anthony A; Högler, Wolfgang; Simmons, Jill H; Gottesman, Gary S; Padidela, Raja; Namba, Noriyuki; Cheong, Hae Il; Nilsson, Ola; Mao, Meng; Chen, Angel; Skrinar, Alison; Roberts, Mary Scott; Imel, Erik A

Sustained Efficacy and Safety of Burosumab, a Monoclonal Antibody to FGF23, in Children With X-Linked Hypophosphatemia

Burosumab(一种针对FGF23的单克隆抗体)在X连锁低磷血症患儿中的持续疗效和安全性

Linglart, Agnès; Imel, Erik A; Whyte, Michael P; Portale, Anthony A; Högler, Wolfgang; Boot, Annemieke M; Padidela, Raja; Van't Hoff, William; Gottesman, Gary S; Chen, Angel; Skrinar, Alison; Scott Roberts, Mary; Carpenter, Thomas O

Vitamin D status and determinants in Indian children and adolescents: a multicentre study

印度儿童和青少年维生素D水平及其决定因素:一项多中心研究

Khadilkar, Anuradha; Kajale, Neha; Oza, Chirantap; Oke, Rashmi; Gondhalekar, Ketan; Patwardhan, Vivek; Khadilkar, Vaman; Mughal, Zulf; Padidela, Raja

Patient-Reported Outcomes from a Randomized, Active-Controlled, Open-Label, Phase 3 Trial of Burosumab Versus Conventional Therapy in Children with X-Linked Hypophosphatemia

一项随机、活性对照、开放标签的3期临床试验中,布罗索单抗与常规疗法治疗X连锁低磷血症患儿的患者报告结局

Padidela, Raja; Whyte, Michael P; Glorieux, Francis H; Munns, Craig F; Ward, Leanne M; Nilsson, Ola; Portale, Anthony A; Simmons, Jill H; Namba, Noriyuki; Cheong, Hae Il; Pitukcheewanont, Pisit; Sochett, Etienne; Högler, Wolfgang; Muroya, Koji; Tanaka, Hiroyuki; Gottesman, Gary S; Biggin, Andrew; Perwad, Farzana; Williams, Angela; Nixon, Annabel; Sun, Wei; Chen, Angel; Skrinar, Alison; Imel, Erik A

Metabolic bone disease of prematurity-National survey of current neonatal and paediatric endocrine approaches

早产儿代谢性骨病——当前新生儿和儿科内分泌治疗方法的全国性调查

Chinoy, Amish; Mughal, Mohammed Zulf; Padidela, Raja