日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Massively parallel reporter assays and mouse transgenic assays provide correlated and complementary information about neuronal enhancer activity.

大规模平行报告基因检测和转基因小鼠检测提供了关于神经元增强子活性的相关和互补信息

Kosicki Michael, Laboy Cintrón Dianne, Keukeleire Pia, Schubach Max, Page Nicholas F, Georgakopoulos-Soares Ilias, Akiyama Jennifer A, Plajzer-Frick Ingrid, Novak Catherine S, Kato Momoe, Hunter Riana D, von Maydell Kianna, Barton Sarah, Godfrey Patrick, Beckman Erik, Sanders Stephan J, Kircher Martin, Pennacchio Len A, Ahituv Nadav

Large-scale discovery of neural enhancers for cis-regulation therapies

大规模发现用于顺式调控疗法的神经增强剂

McDiarmid, Troy A; Page, Nicholas F; Chardon, Florence M; Daza, Riza M; Chen, George T; Kosicki, Michael; James, Lucas M; Nourie, Hannah C; Laboy-Cintrón, Dianne; Lee, Arthur S; Vij, Paula; Calderon, Diego; Lalanne, Jean-Benoît; Martin, Beth K; Fink, Kyle; Talkowski, Michael E; Muotri, Alysson R; Philpot, Benjamin D; Pennacchio, Len A; Geschwind, Daniel H; Sanders, Stephan J; Ahituv, Nadav; Shendure, Jay

Degraded sensory coding in a mouse model of Scn2a-related disorder and its rescue by CRISPRa gene activation.

Scn2a相关疾病小鼠模型中的感觉编码退化及其通过CRISPRa基因激活的挽救。

Vandemark Kaeli, Monday Hannah R, Rodriguez Lucia, Zhao Manya, Lee Meeseo, Ahituv Amit, Satapathy Anwita, Page Nicholas F, An Kelly, Hamada Elizabeth, Ahituv Nadav, Bender Kevin J, Feldman Daniel E

Multiplex, single-cell CRISPRa screening for cell type specific regulatory elements

多重单细胞 CRISPR 筛选,用于检测细胞类型特异性调控元件

Chardon, Florence M; McDiarmid, Troy A; Page, Nicholas F; Daza, Riza M; Martin, Beth; Domcke, Silvia; Regalado, Samuel G; Lalanne, Jean-Benoît; Calderon, Diego; Li, Xiaoyi; Starita, Lea M; Sanders, Stephan J; Ahituv, Nadav; Shendure, Jay

Alterations in Retrotransposition, Synaptic Connectivity, and Myelination Implicated by Transcriptomic Changes Following Maternal Immune Activation in Nonhuman Primates.

非人灵长类动物母体免疫激活后转录组变化所揭示的逆转录转座、突触连接和髓鞘形成的变化

Page Nicholas F, Gandal Michael J, Estes Myka L, Cameron Scott, Buth Jessie, Parhami Sepideh, Ramaswami Gokul, Murray Karl, Amaral David G, Van de Water Judy A, Schumann Cynthia M, Carter Cameron S, Bauman Melissa D, McAllister A Kimberley, Geschwind Daniel H