Evaluation of engineered AAV capsids for hepatic factor IX gene transfer in murine and canine models.
在小鼠和犬模型中评估工程化 AAV 衣壳对肝因子 IX 基因转移的作用
期刊:Journal of Translational Medicine
影响因子:7.5
doi:10.1186/s12967-017-1200-1
Markusic David M, Nichols Timothy C, Merricks Elizabeth P, Palaschak Brett, Zolotukhin Irene, Marsic Damien, Zolotukhin Sergei, Srivastava Arun, Herzog Roland W