日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Gene Therapy-Induced Antigen-Specific Tregs Inhibit Neuro-inflammation and Reverse Disease in a Mouse Model of Multiple Sclerosis

基因治疗诱导的抗原特异性调节性T细胞抑制神经炎症并逆转多发性硬化症小鼠模型中的疾病

Keeler, Geoffrey D; Kumar, Sandeep; Palaschak, Brett; Silverberg, Emily L; Markusic, David M; Jones, Noah T; Hoffman, Brad E

Evaluation of engineered AAV capsids for hepatic factor IX gene transfer in murine and canine models.

在小鼠和犬模型中评估工程化 AAV 衣壳对肝因子 IX 基因转移的作用

Markusic David M, Nichols Timothy C, Merricks Elizabeth P, Palaschak Brett, Zolotukhin Irene, Marsic Damien, Zolotukhin Sergei, Srivastava Arun, Herzog Roland W

An Immune-Competent Murine Model to Study Elimination of AAV-Transduced Hepatocytes by Capsid-Specific CD8(+) T Cells.

利用免疫功能健全的小鼠模型研究衣壳特异性 CD8(+) T 细胞清除 AAV 转导的肝细胞

Palaschak Brett, Marsic Damien, Herzog Roland W, Zolotukhin Sergei, Markusic David M