日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A combinatorial synthetic strategy for developing genome-editing protein-delivery agents targeting mouse retina

一种用于开发靶向小鼠视网膜的基因组编辑蛋白递送载体的组合合成策略

Zhang, Jianye; Hołubowicz, Rafał; Smidak, Roman; Hu, Yulun; Du, Samuel W; Felgner, Jiin H; Palczewska, Grazyna; Rodrigues Menezes, Carolline; Risaliti, Eleonora; Dong, Zhiqian; Ma, Xiuli; Shayegan, Mojtaba H; Chen, Paul Z; Xing, Li; Hołubowicz, Maria; Li, Bowen; Liu, David R; Felgner, Philip L; Tochtrop, Gregory P; Palczewski, Krzysztof

Retinol tracing within murine neural retina reveals cell type-specific retinol transport and distribution

小鼠神经视网膜内视黄醇示踪揭示了细胞类型特异性的视黄醇运输和分布

Engfer, Zachary J; Palczewska, Grazyna; Du, Samuel W; Zhang, Jianye; Dong, Zhiqian; Menezes, Carolline Rodrigues; Wang, Jun; Shao, Jianming; Tucker, Budd A; Mullins, Robert F; Chen, Rui; Kiser, Philip D; Palczewski, Krzysztof

Bi-allelic variants in FSD1L cause retinitis pigmentosa with or without neurological involvement

FSD1L基因的双等位基因变异会导致视网膜色素变性,伴或不伴神经系统受累。

Lin, Siying; Cancellieri, Francesca; Cao, Yexuan; Lotery, Andrew J; Moye, Abigail R; Vaclavik, Veronika; Perren, Fabienne; Poplawski, Andrzej B; Schiff, Elena R; Ullah, Mukhtar; Iglesias-Romero, Ana Belen; Kaminska, Karolina; Jestin, Aleksandr; Folcher, Marc; Wallerich, Sandrine; Ribeiro, Mariana M; Hahaut, Vincent; Picelli, Simone; Mustafi, Debarshi; Tworak, Aleksander; Smidak, Roman; Li, Yumei; Lu, Jiaxiong; Wang, Meng; Mahroo, Omar A; Borooah, Shyamanga; Quinodoz, Mathieu; Palczewski, Krzysztof; Webster, Andrew R; Rivolta, Carlo; Chen, Rui; Arno, Gavin

Lipid-nanoparticle-mediated base editing of the trabecular meshwork rescues glaucoma in vivo.

脂质纳米颗粒介导的小梁网碱基编辑可挽救体内青光眼。

Kaipa Balasankara Reddy, Li Linya, Gopalakrishnan Prakadeeswari, Du Samuel, Felgner Jiin, Palczewski Krzysztof, Felgner Philip, Zode Gulab S

Age-Driven Lipid Remodeling Activates Lysosome-Mediated Plasma Membrane Repair

年龄驱动的脂质重塑激活溶酶体介导的质膜修复

Tom, Emily; Gao, Fangyuan; Franco, Carolina N; Wong, Adrian; Kemmerer, Nathan; Wang, Zichen; Xu, Qianlan; Zhuang, Yinyin; Du, Samuel W; Palczewska, Grazyna; Palczewski, Krzysztof; Budin, Itay; Shi, Xiaoyu; Bonilha, Vera L; Schöeneberg, Johannes; Wahlin, Karl J; Albrecht, Lauren V; Skowronska-Krawczyk, Dorota

Synthetic lethality of mRNA quality control complexes in cancer

癌症中 mRNA 质量控制复合物的合成致死率

Vivian Prindle #, Adam E Richardson #, Kimberly R Sher #, Sarah Kongpachith, Kaitlin Kentala, Sakina Petiwala, Dong Cheng, Deborah Widomski, Phuong Le, Maricel Torrent, Anlu Chen, Stephen Walker, Marianne B Palczewski, Diya Mitra, Vlasios Manaves, Xu Shi, Charles Lu, Stephanie Sandoval, Zoltan Dezso

Safer and efficient base editing and prime editing via ribonucleoproteins delivered through optimized lipid-nanoparticle formulations

通过优化的脂质纳米颗粒制剂递送核糖核蛋白,实现更安全高效的碱基编辑和先导编辑

Rafał Hołubowicz #,Samuel W Du #,Jiin Felgner #,Roman Smidak,Elliot H Choi,Grazyna Palczewska,Carolline Rodrigues Menezes,Zhiqian Dong,Fangyuan Gao,Omar Medani,Alexander L Yan,Maria W Hołubowicz,Paul Z Chen,Marco Bassetto,Eleonora Risaliti,David Salom,J Noah Workman,Philip D Kiser,Andrzej T Foik,David C Lyon,Gregory A Newby,David R Liu,Philip L Felgner,Krzysztof Palczewski

Nitric oxide inhibits ten-eleven translocation DNA demethylases to regulate 5mC and 5hmC across the genome

一氧化氮抑制ten-eleven translocation DNA去甲基化酶,从而调节基因组中的5mC和5hmC水平

Marianne B Palczewski ,Hannah Petraitis Kuschman ,Brian M Hoffman ,Venkatesan Kathiresan ,Hao Yang ,Sharon A Glynn ,David L Wilson ,Eric T Kool ,William R Montfort ,Jenny Chang ,Aydolun Petenkaya ,Constantinos Chronis ,Thomas R Cundari ,Sushma Sappa ,Kabirul Islam ,Daniel W McVicar ,Yu Fan ,Qingrong Chen ,Daoud Meerzaman ,Michael Sierk ,Douglas D Thomas

Integrin Trafficking, Fibronectin Architecture, and Glomerular Injury upon Adiponectin Receptor 1 Depletion.

脂联素受体 1 耗竭后整合素运输、纤连蛋白结构和肾小球损伤

Lindfors Sonja, Schmotz Constanze, Lewandowski Dominik, Hau Annika, Saikko Leena, Lehtonen Eero, Majaniemi Ville, Karhe Minna, Naams Jette-Britt, Nisen Harry, Tienari Jukka, Saleem Moin A, Pfeil Katharina, Bugger Heiko, Pietiläinen Kirsi H, Mirtti Tuomas, Palczewski Krzysztof, Lehtonen Sanna

TIGER: A tdTomato in vivo genome-editing reporter mouse for investigating precision-editor delivery approaches

TIGER:一种用于研究精准编辑递送方法的tdTomato体内基因组编辑报告小鼠

Du, Samuel W; Palczewska, Grazyna; Dong, Zhiqian; Lauterborn, Julie C; Kaipa, Balasankara Reddy; Yan, Alexander L; Hołubowicz, Rafał; Ha, Siyoung; Chen, Paul Z; Gall, Christine M; Zode, Gulab; Liu, David R; Palczewski, Krzysztof