Intravenous lipid-siRNA conjugate mediates gene silencing at the blood-brain barrier and blood-CSF barrier.
静脉注射脂质-siRNA偶联物可介导血脑屏障和血脑脊液屏障处的基因沉默
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doi:10.1101/2025.03.14.642142
Sorets Alexander G, Schwensen Katrina R, Francini Nora, Kjar Andrew, Lyons Sarah, Park Joshua C, Palmer Dillon, Abdulrahman Adam M, Cowell Rebecca P, Katdare Ketaki A, Hoogenboezem Ella N, Wang Angela, Dani Neil, Duvall Craig L, Lippmann Ethan S