日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Functional abnormalities in induced Pluripotent Stem Cell-derived cardiomyocytes generated from titin-mutated patients with dilated cardiomyopathy.

从肌联蛋白突变扩张型心肌病患者体内诱导多能干细胞衍生的心肌细胞的功能异常

Schick Revital, Mekies Lucy N, Shemer Yuval, Eisen Binyamin, Hallas Tova, Ben Jehuda Ronen, Ben-Ari Meital, Szantai Agnes, Willi Lubna, Shulman Rita, Gramlich Michael, Pane Luna Simona, My Ilaria, Freimark Dov, Murgia Marta, Santamaria Gianluca, Gherghiceanu Mihaela, Arad Michael, Moretti Alessandra, Binah Ofer

Subtype-specific promoter-driven action potential imaging for precise disease modelling and drug testing in hiPSC-derived cardiomyocytes

利用亚型特异性启动子驱动的动作电位成像技术,在hiPSC衍生的心肌细胞中进行精确的疾病建模和药物测试

Chen, Zhifen; Xian, Wenying; Bellin, Milena; Dorn, Tatjana; Tian, Qinghai; Goedel, Alexander; Dreizehnter, Lisa; Schneider, Christine M; Ward-van Oostwaard, Dorien; Ng, Judy King Man; Hinkel, Rabea; Pane, Luna Simona; Mummery, Christine L; Lipp, Peter; Moretti, Alessandra; Laugwitz, Karl-Ludwig; Sinnecker, Daniel

Antisense-mediated exon skipping: a therapeutic strategy for titin-based dilated cardiomyopathy

反义介导的外显子跳跃:一种治疗肌联蛋白相关扩张型心肌病的策略

Gramlich, Michael; Pane, Luna Simona; Zhou, Qifeng; Chen, Zhifen; Murgia, Marta; Schötterl, Sonja; Goedel, Alexander; Metzger, Katja; Brade, Thomas; Parrotta, Elvira; Schaller, Martin; Gerull, Brenda; Thierfelder, Ludwig; Aartsma-Rus, Annemieke; Labeit, Siegfried; Atherton, John J; McGaughran, Julie; Harvey, Richard P; Sinnecker, Daniel; Mann, Matthias; Laugwitz, Karl-Ludwig; Gawaz, Meinrad Paul; Moretti, Alessandra