Long term disease burden post-transplantation: three decades of observations in 25 Hurler patients successfully treated with hematopoietic stem cell transplantation (HSCT)
移植后长期疾病负担:25 例接受造血干细胞移植 (HSCT) 成功治疗的 Hurler 病患者三十年观察
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-020-01644-w
Guffon, N; Pettazzoni, M; Pangaud, N; Garin, C; Lina-Granade, G; Plault, C; Mottolese, C; Froissart, R; Fouilhoux, A