A humanized mouse model for adeno-associated viral gene therapy
用于腺相关病毒基因治疗的人源化小鼠模型
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-024-46017-0
Mercedes Barzi # ,Tong Chen # ,Trevor J Gonzalez ,Francis P Pankowicz ,Seh Hoon Oh ,Helen L Streff ,Alan Rosales ,Yunhan Ma ,Sabrina Collias ,Sarah E Woodfield ,Anna Mae Diehl ,Sanjeev A Vasudevan ,Thao N Galvan ,John Goss ,Charles A Gersbach ,Beatrice Bissig-Choisat ,Aravind Asokan ,Karl-Dimiter Bissig