日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CRISPR/Cas9 gene therapy increases the risk of tumorigenesis in the mouse model of hereditary tyrosinemia type I.

CRISPR/Cas9 基因疗法增加了 I 型遗传性酪氨酸血症小鼠模型发生肿瘤的风险

Chen Tong, Barzi Mercedes, Furey Nika, Kim Hyunjae R, Pankowicz Francis P, Legras Xavier, Elsea Sara H, Hurley Ayrea E, Yang Diane, Wheeler David A, Borowiak Malgorzata, Bissig-Choisat Beatrice, Sumazin Pavel, Bissig Karl-Dimiter

A humanized mouse model for adeno-associated viral gene therapy

用于腺相关病毒基因治疗的人源化小鼠模型

Mercedes Barzi # ,Tong Chen # ,Trevor J Gonzalez ,Francis P Pankowicz ,Seh Hoon Oh ,Helen L Streff ,Alan Rosales ,Yunhan Ma ,Sabrina Collias ,Sarah E Woodfield ,Anna Mae Diehl ,Sanjeev A Vasudevan ,Thao N Galvan ,John Goss ,Charles A Gersbach ,Beatrice Bissig-Choisat ,Aravind Asokan ,Karl-Dimiter Bissig

A hepatitis B virus transgenic mouse model with a conditional, recombinant, episomal genome

一种具有条件性重组游离基因组的乙型肝炎病毒转基因小鼠模型

Kruse, Robert L; Barzi, Mercedes; Legras, Xavier; Pankowicz, Francis P; Furey, Nika; Liao, Lan; Xu, Janming; Bissig-Choisat, Beatrice; Slagle, Betty L; Bissig, Karl-Dimiter

Rapid Disruption of Genes Specifically in Livers of Mice Using Multiplex CRISPR/Cas9 Editing

利用多重CRISPR/Cas9编辑技术快速特异性地破坏小鼠肝脏中的基因

Pankowicz, Francis P; Barzi, Mercedes; Kim, Kang Ho; Legras, Xavier; Martins, Celeste Santos; Wooton-Kee, Clavia Ruth; Lagor, William R; Marini, Juan C; Elsea, Sarah H; Bissig-Choisat, Beatrice; Moore, David D; Bissig, Karl-Dimiter

P450-Humanized and Human Liver Chimeric Mouse Models for Studying Xenobiotic Metabolism and Toxicity

用于研究异生物质代谢和毒性的P450人源化和人肝嵌合小鼠模型

Bissig, Karl-Dimiter; Han, Weiguo; Barzi, Mercedes; Kovalchuk, Nataliia; Ding, Liang; Fan, Xiaoyu; Pankowicz, Francis P; Zhang, Qing-Yu; Ding, Xinxin

CRISPR/Cas9: at the cutting edge of hepatology

CRISPR/Cas9:肝病学的前沿技术

Pankowicz, Francis P; Jarrett, Kelsey E; Lagor, William R; Bissig, Karl-Dimiter

A novel humanized mouse lacking murine P450 oxidoreductase for studying human drug metabolism

一种缺乏小鼠 P450 氧化还原酶的新型人源化小鼠,用于研究人类药物代谢

Mercedes Barzi, Francis P Pankowicz, Barry Zorman, Xing Liu, Xavier Legras, Diane Yang, Malgorzata Borowiak, Beatrice Bissig-Choisat, Pavel Sumazin, Feng Li, Karl-Dimiter Bissig

In Situ Liver Expression of HBsAg/CD3-Bispecific Antibodies for HBV Immunotherapy

乙肝病毒免疫治疗中HBsAg/CD3双特异性抗体的原位肝脏表达

Kruse, Robert L; Shum, Thomas; Legras, Xavier; Barzi, Mercedes; Pankowicz, Frank P; Gottschalk, Stephen; Bissig, Karl-Dimiter

Reprogramming metabolic pathways in vivo with CRISPR/Cas9 genome editing to treat hereditary tyrosinaemia

利用 CRISPR/Cas9 基因组编辑技术在体内重编程代谢途径以治疗遗传性酪氨酸血症

Francis P Pankowicz, Mercedes Barzi, Xavier Legras, Leroy Hubert, Tian Mi, Julie A Tomolonis, Milan Ravishankar, Qin Sun, Diane Yang, Malgorzata Borowiak, Pavel Sumazin, Sarah H Elsea, Beatrice Bissig-Choisat, Karl-Dimiter Bissig

Development and rescue of human familial hypercholesterolaemia in a xenograft mouse model

在异种移植小鼠模型中建立和挽救人类家族性高胆固醇血症

Beatrice Bissig-Choisat ,Lili Wang ,Xavier Legras ,Pradip K Saha ,Leon Chen ,Peter Bell ,Francis P Pankowicz ,Matthew C Hill ,Mercedes Barzi ,Claudia Kettlun Leyton ,Hon-Chiu Eastwood Leung ,Robert L Kruse ,Ryan W Himes ,John A Goss ,James M Wilson ,Lawrence Chan ,William R Lagor ,Karl-Dimiter Bissig