日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Limiting endosomal damage sensing reduces inflammation triggered by lipid nanoparticle endosomal escape.

限制内体损伤感知可减少脂质纳米颗粒内体逃逸引发的炎症

Omo-Lamai Serena, Wang Yufei, Patel Manthan N, Milosavljevic Aleksa, Zuschlag Daniel, Poddar Subhajit, Wu Jichuan, Wang Liuqian, Dong Fengyi, Espy Carolann, Majumder Aparajeeta, Essien Eno-Obong, Shen Mengwen, Channer Breana, Papp Tyler E, Tobin Michael, Maheshwari Rhea, Jeong Sumin, Patel Sofia, Shah Anit, Murali Shruthi, Chase Liam S, Zamora Marco E, Arral Mariah L, Marcos-Contreras Oscar A, Myerson Jacob W, Hunter Christopher A, Discher Dennis, Gaskill Peter J, Tsourkas Andrew, Muzykantov Vladimir R, Brodsky Igor, Shin Sunny, Whitehead Kathryn A, Parhiz Hamideh, Katzen Jeremy, Miner Jonathan J, Trauner Dirk, Brenner Jacob S

An erythroid-specific lentiviral vector improves anemia and iron metabolism in a new model of XLSA

一种红细胞特异性慢病毒载体可改善XLSA新模型中的贫血和铁代谢。

Castruccio Castracani, Carlo; Breda, Laura; Papp, Tyler E; Guerra, Amaliris; Radaelli, Enrico; Assenmacher, Charles-Antoine; Finesso, Giovanni; Mui, Barbara L; Tam, Ying K; Fontana, Simona; Riganti, Chiara; Fiorito, Veronica; Petrillo, Sara; Tolosano, Emanuela; Parhiz, Hamideh; Rivella, Stefano

CD47 peptide-cloaked lipid nanoparticles promote cell-specific mRNA delivery

CD47肽包裹的脂质纳米颗粒促进细胞特异性mRNA递送

Papp, Tyler Ellis; Zeng, Jianhao; Shahnawaz, Hamna; Akyianu, Awurama; Breda, Laura; Yadegari, Amir; Steward, Joseph; Shi, Ruiqi; Li, Qin; Mui, Barbara L; Tam, Ying K; Weissman, Drew; Rivella, Stefano; Shuvaev, Vladimir; Muzykantov, Vladimir R; Parhiz, Hamideh

Targeted lipid nanoparticles containing IL-10 mRNA improve outcomes in experimental intracerebral hemorrhage

含有IL-10 mRNA的靶向脂质纳米颗粒可改善实验性脑出血的预后

Reyes-Esteves, Sahily; Majumder, Aparajeeta; Marzolini, Nicolas; Zamora, Marco E; Jeong, Soomin; Wang, Yufei; Patel, Manthan N; Espy, Carolann; Papp, Tyler Ellis; Akyianu, Awurama; Nong, Jia; Messe, Lawson; Omo-Lamai, Serena; Parhiz, Hamideh; Myerson, Jacob W; Marcos-Contreras, Oscar A; Brenner, Jacob S

Systemic delivery of biotherapeutic RNA to the myocardium transiently modulates cardiac contractility in vivo.

将生物治疗性 RNA 系统性输送至心肌可暂时性地调节体内心脏收缩力

Shuvaev Vladimir V, Tam Ying K, Lee Benjamin W, Myerson Jacob W, Herbst Alan, Kiseleva Raisa Yu, Glassman Patrick M, Parhiz Hamideh, Alameh Mohamad-Gabriel, Pardi Norbert, Muramatsu Hiromi, Shuvaeva Tea I, Arguiri Evguenia, Marcos-Contreras Oscar A, Hood Elizabeth D, Brysgel Taylor V, Nong Jia, Papp Tyler E, Eaton Deborah M, Riley Rachel, Palanki Rohan, Musunuru Kiran, Brenner Jacob S, Mitchell Michael J, Ferrari Victor A, Mui Barbara L, Semple Sean C, Weppler Sherry A, Atluri Pavan, Margulies Kenneth B, Weissman Drew, Muzykantov Vladimir R

In Situ Tumor Vaccination Using Lipid Nanoparticles to Deliver Interferon-β mRNA Cargo.

利用脂质纳米颗粒递送干扰素-β mRNA 载荷进行原位肿瘤疫苗接种

Kimura Kenji, Aicher Aidan, Niemeyer Emma, Areesawangkit Phurin, Tilsed Caitlin, Fong Karen P, Papp Tyler E, Albelda Steven M, Parhiz Hamideh, Predina Jarrod D

In vivo anti-FAP CAR T therapy reduces fibrosis and restores liver homeostasis in metabolic dysfunction-associated steatohepatitis

体内抗FAP CAR-T疗法可减少代谢功能障碍相关性脂肪性肝炎中的纤维化并恢复肝脏稳态

Yashaswini, Chittampalli N; Cogliati, Bruno; Qin, Tianyue; To, Tran; Williamson, Thomas; Papp, Tyler E; Li, Kenneth; Rasul, Raisa; Chen, Li; Lightstone, Adi; Aghajanian, Haig; Parhiz, Hamideh; Wang, Shuang; Rurik, Joel G; Epstein, Jonathan A; Friedman, Scott L

Targeted lipid nanoparticles containing IL-10 mRNA improve outcomes in experimental intracerebral hemorrhage.

含有IL-10 mRNA的靶向脂质纳米颗粒可改善实验性脑出血的预后

Reyes-Esteves Sahily, Majumder Aparajeeta, Marzolini Nicolas, Zamora Marco, Wang Yufei, Espy Carolann, Papp Tyler Ellis, Akyianu Awurama, Nong Jia, Messe Lawson, Omo-Lamai Serena, Parhiz Hamideh, Myerson Jacob, Marcos-Contreras Oscar, Brenner Jacob

SRSF3 knockdown-induced cellular senescence as a possible therapeutic strategy for non-small cell lung cancer.

SRSF3 敲低诱导细胞衰老作为非小细胞肺癌的一种潜在治疗策略

Nakamichi Shinji, von Muhlinen Natalia, Yamada Leo, Melamed Jilian R, Papp Tyler E, Parhiz Hamideh, Weissman Drew, Horikawa Izumi, Harris Curtis C

Use of HSC-targeted LNP to generate a mouse model of lethal α-thalassemia and treatment via lentiviral gene therapy

利用靶向造血干细胞的脂质纳米颗粒构建致死性α-地中海贫血小鼠模型,并通过慢病毒基因治疗进行治疗。

Chappell, Maxwell E; Breda, Laura; Tricoli, Lucas; Guerra, Amaliris; Jarocha, Danuta; Castruccio Castracani, Carlo; Papp, Tyler E; Tanaka, Naoto; Hamilton, Nolan; Triebwasser, Michael P; Ghiaccio, Valentina; Fedorky, Megan T; Gollomp, Kandace L; Bochenek, Veronica; Roche, Aoife M; Everett, John K; Cook, Emma J; Bushman, Frederic D; Teawtrakul, Nattiya; Glentis, Stavros; Kattamis, Antonis; Mui, Barbara L; Tam, Ying K; Weissman, Drew; Abdulmalik, Osheiza; Parhiz, Hamideh; Rivella, Stefano