日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Shorter Phosphorodiamidate Morpholino Splice-Switching Oligonucleotides May Increase Exon-Skipping Efficacy in DMD

较短的磷酰二胺吗啉代剪接转换寡核苷酸可能提高杜氏肌营养不良症(DMD)中外显子跳跃的效率。

Akpulat, Ugur; Wang, Haicui; Becker, Kerstin; Contreras, Adriana; Partridge, Terence A; Novak, James S; Cirak, Sebahattin

The macrophage as a Trojan horse for antisense oligonucleotide delivery

巨噬细胞作为反义寡核苷酸递送的特洛伊木马

Novak, James S; Jaiswal, Jyoti K; Partridge, Terence A

Asynchronous remodeling is a driver of failed regeneration in Duchenne muscular dystrophy

异步重塑是杜氏肌营养不良症再生失败的驱动因素。

Dadgar, Sherry; Wang, Zuyi; Johnston, Helen; Kesari, Akanchha; Nagaraju, Kanneboyina; Chen, Yi-Wen; Hill, D Ashley; Partridge, Terence A; Giri, Mamta; Freishtat, Robert J; Nazarian, Javad; Xuan, Jianhua; Wang, Yue; Hoffman, Eric P

Survival motor neuron protein deficiency impairs myotube formation by altering myogenic gene expression and focal adhesion dynamics

运动神经元存活蛋白缺乏会通过改变肌源性基因表达和黏着斑动力学来损害肌管形成。

Bricceno, Katherine V; Martinez, Tara; Leikina, Evgenia; Duguez, Stephanie; Partridge, Terence A; Chernomordik, Leonid V; Fischbeck, Kenneth H; Sumner, Charlotte J; Burnett, Barrington G

The mdx mouse model as a surrogate for Duchenne muscular dystrophy

mdx小鼠模型作为杜氏肌营养不良症的替代模型

Partridge, Terence A

Myogenesis in dysferlin-deficient myoblasts is inhibited by an intrinsic inflammatory response

肌纤维蛋白缺陷型成肌细胞的肌生成受到内在炎症反应的抑制

Cohen, Tatiana V; Cohen, Jonathan E; Partridge, Terence A

The isolated muscle fibre as a model of disuse atrophy: characterization using PhAct, a method to quantify f-actin

以分离的肌纤维作为废用性萎缩的模型:利用 PhAct 方法(一种定量 f-肌动蛋白的方法)进行表征

Duddy, William J; Cohen, Tatiana; Duguez, Stephanie; Partridge, Terence A

Preclinical drug trials in the mdx mouse: assessment of reliable and sensitive outcome measures

mdx小鼠临床前药物试验:可靠且灵敏的结局指标评估

Spurney, Christopher F; Gordish-Dressman, Heather; Guerron, Alfredo D; Sali, Arpana; Pandey, Gouri S; Rawat, Rashmi; Van Der Meulen, Jack H; Cha, Hee-Jae; Pistilli, Emidio E; Partridge, Terence A; Hoffman, Eric P; Nagaraju, Kanneboyina

A renaissance for antisense oligonucleotide drugs in neurology: exon skipping breaks new ground

神经病学领域反义寡核苷酸药物的复兴:外显子跳跃开辟新天地

Yokota, Toshifumi; Takeda, Shin'ichi; Lu, Qi-Long; Partridge, Terence A; Nakamura, Akinori; Hoffman, Eric P

Myogenic cell proliferation and generation of a reversible tumorigenic phenotype are triggered by preirradiation of the recipient site.

受体部位预先照射可触发肌源性细胞增殖和可逆性肿瘤表型的产生

Morgan Jennifer E, Gross Jacqueline G, Pagel Charles N, Beauchamp Jonathan R, Fassati Ariberto, Thrasher Adrian J, Di Santo James P, Fisher Ivan B, Shiwen Xu, Abraham David J, Partridge Terence A