Targeted gene addition in human CD34(+) hematopoietic cells for correction of X-linked chronic granulomatous disease
靶向基因添加至人类CD34(+)造血细胞以纠正X连锁慢性肉芽肿病
期刊:Nature Biotechnology
影响因子:41.7
doi:10.1038/nbt.3513
De Ravin, Suk See; Reik, Andreas; Liu, Pei-Qi; Li, Linhong; Wu, Xiaolin; Su, Ling; Raley, Castle; Theobald, Narda; Choi, Uimook; Song, Alexander H; Chan, Andy; Pearl, Jocelynn R; Paschon, David E; Lee, Janet; Newcombe, Hannah; Koontz, Sherry; Sweeney, Colin; Shivak, David A; Zarember, Kol A; Peshwa, Madhusudan V; Gregory, Philip D; Urnov, Fyodor D; Malech, Harry L