日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Humanized Mouse Model of HIV-1 Latency with Enrichment of Latent Virus in PD-1(+) and TIGIT(+) CD4 T Cells

人源化小鼠 HIV-1 潜伏模型,PD-1(+) 和 TIGIT(+) CD4 T 细胞中潜伏病毒富集

Llewellyn, George N; Seclén, Eduardo; Wietgrefe, Stephen; Liu, Siyu; Chateau, Morgan; Pei, Hua; Perkey, Katherine; Marsden, Matthew D; Hinkley, Sarah J; Paschon, David E; Holmes, Michael C; Zack, Jerome A; Louie, Stan G; Haase, Ashley T; Cannon, Paula M

Targeted gene addition in human CD34(+) hematopoietic cells for correction of X-linked chronic granulomatous disease

靶向基因添加至人类CD34(+)造血细胞以纠正X连锁慢性肉芽肿病

De Ravin, Suk See; Reik, Andreas; Liu, Pei-Qi; Li, Linhong; Wu, Xiaolin; Su, Ling; Raley, Castle; Theobald, Narda; Choi, Uimook; Song, Alexander H; Chan, Andy; Pearl, Jocelynn R; Paschon, David E; Lee, Janet; Newcombe, Hannah; Koontz, Sherry; Sweeney, Colin; Shivak, David A; Zarember, Kol A; Peshwa, Madhusudan V; Gregory, Philip D; Urnov, Fyodor D; Malech, Harry L

Functional footprinting of regulatory DNA

调控DNA的功能足迹分析

Vierstra, Jeff; Reik, Andreas; Chang, Kai-Hsin; Stehling-Sun, Sandra; Zhou, Yuanyue; Hinkley, Sarah J; Paschon, David E; Zhang, Lei; Psatha, Nikoletta; Bendana, Yuri R; O'Neil, Colleen M; Song, Alexander H; Mich, Andrea K; Liu, Pei-Qi; Lee, Gary; Bauer, Daniel E; Holmes, Michael C; Orkin, Stuart H; Papayannopoulou, Thalia; Stamatoyannopoulos, George; Rebar, Edward J; Gregory, Philip D; Urnov, Fyodor D; Stamatoyannopoulos, John A

Targeted correction and restored function of the CFTR gene in cystic fibrosis induced pluripotent stem cells

针对囊性纤维化诱导多能干细胞中CFTR基因的靶向校正和功能恢复

Crane, Ana M; Kramer, Philipp; Bui, Jacquelin H; Chung, Wook Joon; Li, Xuan Shirley; Gonzalez-Garay, Manuel L; Hawkins, Finn; Liao, Wei; Mora, Daniela; Choi, Sangbum; Wang, Jianbin; Sun, Helena C; Paschon, David E; Guschin, Dmitry Y; Gregory, Philip D; Kotton, Darrell N; Holmes, Michael C; Sorscher, Eric J; Davis, Brian R

Editing T cell specificity towards leukemia by zinc finger nucleases and lentiviral gene transfer

利用锌指核酸酶和慢病毒基因转移编辑T细胞对白血病的特异性

Provasi, Elena; Genovese, Pietro; Lombardo, Angelo; Magnani, Zulma; Liu, Pei-Qi; Reik, Andreas; Chu, Victoria; Paschon, David E; Zhang, Lei; Kuball, Jurgen; Camisa, Barbara; Bondanza, Attilio; Casorati, Giulia; Ponzoni, Maurilio; Ciceri, Fabio; Bordignon, Claudio; Greenberg, Philip D; Holmes, Michael C; Gregory, Philip D; Naldini, Luigi; Bonini, Chiara

In vivo genome editing restores haemostasis in a mouse model of haemophilia

体内基因组编辑可恢复血友病小鼠模型的止血功能

Li, Hojun; Haurigot, Virginia; Doyon, Yannick; Li, Tianjian; Wong, Sunnie Y; Bhagwat, Anand S; Malani, Nirav; Anguela, Xavier M; Sharma, Rajiv; Ivanciu, Lacramiora; Murphy, Samuel L; Finn, Jonathan D; Khazi, Fayaz R; Zhou, Shangzhen; Paschon, David E; Rebar, Edward J; Bushman, Frederic D; Gregory, Philip D; Holmes, Michael C; High, Katherine A

Targeted gene correction of α1-antitrypsin deficiency in induced pluripotent stem cells

诱导多能干细胞中α1-抗胰蛋白酶缺乏症的靶向基因矫正

Yusa, Kosuke; Rashid, S Tamir; Strick-Marchand, Helene; Varela, Ignacio; Liu, Pei-Qi; Paschon, David E; Miranda, Elena; Ordóñez, Adriana; Hannan, Nicholas R F; Rouhani, Foad J; Darche, Sylvie; Alexander, Graeme; Marciniak, Stefan J; Fusaki, Noemi; Hasegawa, Mamoru; Holmes, Michael C; Di Santo, James P; Lomas, David A; Bradley, Allan; Vallier, Ludovic

Efficient targeted gene disruption in the soma and germ line of the frog Xenopus tropicalis using engineered zinc-finger nucleases.

利用工程化锌指核酸酶对非洲爪蟾的体细胞和生殖细胞进行高效的靶向基因破坏

Young John J, Cherone Jennifer M, Doyon Yannick, Ankoudinova Irina, Faraji Farhoud M, Lee Andrew H, Ngo Catherine, Guschin Dmitry Y, Paschon David E, Miller Jeffrey C, Zhang Lei, Rebar Edward J, Gregory Philip D, Urnov Fyodor D, Harland Richard M, Zeitler Bryan

Functional genomics, proteomics, and regulatory DNA analysis in isogenic settings using zinc finger nuclease-driven transgenesis into a safe harbor locus in the human genome

利用锌指核酸酶驱动的转基因技术,在人类基因组的安全港位点进行同源基因组学、蛋白质组学和调控DNA分析

DeKelver, Russell C; Choi, Vivian M; Moehle, Erica A; Paschon, David E; Hockemeyer, Dirk; Meijsing, Sebastiaan H; Sancak, Yasemin; Cui, Xiaoxia; Steine, Eveline J; Miller, Jeffrey C; Tam, Phillip; Bartsevich, Victor V; Meng, Xiangdong; Rupniewski, Igor; Gopalan, Sunita M; Sun, Helena C; Pitz, Kathleen J; Rock, Jeremy M; Zhang, Lei; Davis, Gregory D; Rebar, Edward J; Cheeseman, Iain M; Yamamoto, Keith R; Sabatini, David M; Jaenisch, Rudolf; Gregory, Philip D; Urnov, Fyodor D

An engineered zinc finger protein activator of the endogenous glial cell line-derived neurotrophic factor gene provides functional neuroprotection in a rat model of Parkinson's disease

一种经基因工程改造的锌指蛋白激活剂,可激活内源性胶质细胞系衍生神经营养因子基因,在帕金森病大鼠模型中提供功能性神经保护作用。

Laganiere, Josee; Kells, Adrian P; Lai, Jeffrey T; Guschin, Dmitry; Paschon, David E; Meng, Xiangdong; Fong, Lauren K; Yu, Qi; Rebar, Edward J; Gregory, Philip D; Bankiewicz, Krystof S; Forsayeth, John; Zhang, H Steve