日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Disease Trajectories and Glucocorticoid Exposure in VEXAS Syndrome Treated with Cytokine-Directed Therapies

接受细胞因子靶向治疗的VEXAS综合征患者的疾病轨迹和糖皮质激素暴露情况

Turturice, Benjamin A; Fike, Alice; Patel, Bhavisha A; Groarke, Emma M; Gutierrez-Rodriguez, Fernanda; Stonick, Karyssa; Berrett, Hannah; Liu, Shanni; Darden, Ivana; Quinn, Kaitlin A; Young, Neal S; Grayson, Peter C

Selective Janus kinase inhibitors exhibit different effects in murine immune aplastic anemia

选择性 Janus 激酶抑制剂在小鼠免疫性再生障碍性贫血中表现出不同的作用

Durrani, Jibran; Feng, Xingmin; Wu, Zhijie; Gao, Shouguo; Manley, Ash Lee; Wu, Liangliang; Glass, Joshua; Patel, Bhavisha A; Chen, Jichun; Young, Neal S; Groarke, Emma M

American College of Rheumatology Guidance Statement for Diagnosis and Management of VEXAS Developed by the International VEXAS Working Group Expert Panel

美国风湿病学会关于VEXAS诊断和治疗的指导声明,由国际VEXAS工作组专家组制定

Mekinian, Arsene; Georgin-Lavialle, Sophie; Ferrada, Marcela A; Savic, Sinisa; Koster, Matthew J; Kosmider, Olivier; Comont, Thibault; Heiblig, Mael; Arostegui, Juan I; Bosco, Annmarie; Bourguiba, Rim; Calvo, Katherine R; Cargo, Catherine; Cattaneo, Chiara; Chasset, François; Coelho, Henrique; Campochiaro, Corrado; Crisafulli, Francesca; Ducharme-Benard, Stephanie; Faria, Raquel; Franceschini, Franco; Frassi, Micol; Groarke, Emma M; Gurnari, Carmelo; Hakobyan, Yervand; Jamilloux, Yvan; Jurcut, Ciprian; Kirino, Yohei; Kulasekararaj, Austin; Kunimoto, Hiroyoshi; Madigan, Lauren M; Mann, Heřman F; Marvisi, Chiara; Milchert, Marcin; Morais, Sara; Sockel, Katja; Muratore, Francesco; Nakajima, Hideaki; Patnaik, Mrinal M; Regadas, Luísa; Robin, Marie; Rutgers, Abraham; Salvarani, Carlo; Sammel, Anthony M; Seebach, Joerg; Sujobert, Pierre; Tomelleri, Alessandro; Urbanski, Geoffrey; Vandergheynst, Frédéric; Vieira, Romana; Viswanatha, David S; Więsik-Szewczyk, Ewa; Diral, Elisa; Terrier, Benjamin; Patel, Bhavisha A; Fenaux, Pierre; Grayson, Peter C; Beck, David B

Danazol treatment for telomere biology disorders: long-term results of a phase 1/2 study

达那唑治疗端粒生物学疾病:一项 1/2 期研究的长期结果

Lee, Nicholas C; Gutierrez-Rodrigues, Fernanda; Shalhoub, Ruba; Machado, Tania; Lotter, Jennifer; Alemu, Lemlem; Raffo, Diego Quinones; Paul, Subrata; Kajigaya, Sachiko; Aubert, Geraldine; Wu, Colin O; Young, Neal S; Patel, Bhavisha A; Groarke, Emma M

Hypomethylating agents in vacuoles, E1 enzyme, X-linked, autoinflammatory, somatic syndrome (VEXAS): A systematic review

空泡低甲基化剂、E1酶、X连锁自身炎症性体细胞综合征(VEXAS):系统评价

Hoff, Fieke W; Trikha, Roochi; Groarke, Emma M; Patel, Bhavisha A

Clinical and molecular features of immunodeficiency in patients with telomere biology disorders

端粒生物学障碍患者的免疫缺陷的临床和分子特征

Bazzo Catto, Luiz Fernando; Aggarwal, Nidhi; Shalhoub, Ruba; Ma, Xiaoyang; Darden, Ivana; Machado, Tania; Zhang, Yue; Redekar, Neelam R; Thongon, Natthakan; Colla, Simona; Aubert, Geraldine; Dunbar, Cynthia E; Wu, Colin O; Young, Neal S; Patel, Bhavisha A; Gutierrez-Rodrigues, Fernanda; Groarke, Emma M

Impact of HLA alloimmunization on clinical outcomes of severe aplastic anemia treated with immunosuppressive therapy

HLA同种免疫对接受免疫抑制治疗的重型再生障碍性贫血临床结局的影响

Durrani, Jibran; Chen, Leonard N; Shalhoub, Ruba N; Baez, Valentina; Glass, Joshua; Cha, Nu Ri; Ma, Xiaoyang; Wu, Zhijie; Gao, Shouguo; Lotter, Jennifer; Rios, Olga; Wu, Colin O; Flegel, Willy A; Young, Neal S; Groarke, Emma M; Patel, Bhavisha A

Clonal landscape and clinical outcomes of telomere biology disorders: somatic rescue and cancer mutations

克隆图谱和端粒生物学疾病的临床结果:体细胞拯救和癌症突变

Gutierrez-Rodrigues, Fernanda; Groarke, Emma M; Thongon, Natthakan; Rodriguez-Sevilla, Juan Jose; Catto, Luiz Fernando B; Niewisch, Marena R; Shalhoub, Ruba; McReynolds, Lisa J; Clé, Diego V; Patel, Bhavisha A; Ma, Xiaoyang; Hironaka, Dalton; Donaires, Flávia S; Spitofsky, Nina; Santana, Barbara A; Lai, Tsung-Po; Alemu, Lemlem; Kajigaya, Sachiko; Darden, Ivana; Zhou, Weiyin; Browne, Paul V; Paul, Subrata; Lack, Justin; Young, David J; DiNardo, Courtney D; Aviv, Abraham; Ma, Feiyang; De Oliveira, Michel Michels; de Azambuja, Ana Paula; Dunbar, Cynthia E; Olszewska, Malgorzata; Olivier, Emmanuel; Papapetrou, Eirini P; Giri, Neelam; Alter, Blanche P; Bonfim, Carmem; Wu, Colin O; Garcia-Manero, Guillermo; Savage, Sharon A; Young, Neal S; Colla, Simona; Calado, Rodrigo T

Venous and arterial thrombosis in patients with VEXAS syndrome

VEXAS综合征患者的静脉和动脉血栓形成

Kusne, Yael; Ghorbanzadeh, Atefeh; Dulau-Florea, Alina; Shalhoub, Ruba; Alcedo, Pedro E; Nghiem, Khanh; Ferrada, Marcela A; Hines, Alexander; Quinn, Kaitlin A; Panicker, Sumith R; Ombrello, Amanda K; Reichard, Kaaren; Darden, Ivana; Goodspeed, Wendy; Durrani, Jibran; Wilson, Lorena; Olteanu, Horatiu; Lasho, Terra; Kastner, Daniel L; Warrington, Kenneth J; Mangaonkar, Abhishek; Go, Ronald S; Braylan, Raul C; Beck, David B; Patnaik, Mrinal M; Young, Neal S; Calvo, Katherine R; Casanegra, Ana I; Grayson, Peter C; Koster, Matthew J; Wu, Colin O; Kanthi, Yogendra; Patel, Bhavisha A; Houghton, Damon E; Groarke, Emma M

Clonal haematopoiesis across the age spectrum of vasculitis patients with Takayasu's arteritis, ANCA-associated vasculitis and giant cell arteritis

克隆性造血在患有大动脉炎、ANCA相关性血管炎和巨细胞动脉炎的血管炎患者年龄段中的分布

Gutierrez-Rodrigues, Fernanda; Wells, Kristina V; Jones, Adrianna I; Hironaka, Dalton; Rankin, Cameron; Gadina, Massimo; Sikora, Keith A; Alemu, Lemlem; Calado, Rodrigo T; Quinn, Kaitlin A; Patel, Bhavisha; Young, Neal S; Grayson, Peter C