Endogenous factor VIII synthesis from the intron 22-inverted F8 locus may modulate the immunogenicity of replacement therapy for hemophilia A
来自内含子 22 倒置 F8 基因座的内源性因子 VIII 合成可能会调节血友病 A 替代疗法的免疫原性
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/nm.3270
Gouri Shankar Pandey, Chen Yanover, Lisa M Miller-Jenkins, Susan Garfield, Shelley A Cole, Joanne E Curran, Eric K Moses, Natalia Rydz, Vijaya Simhadri, Chava Kimchi-Sarfaty, David Lillicrap, Kevin R Viel, Teresa M Przytycka, Glenn F Pierce, Tom E Howard, Zuben E Sauna; PATH (Personalized Alternativ