日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A combinatorial synthetic strategy for developing genome-editing protein-delivery agents targeting mouse retina

一种用于开发靶向小鼠视网膜的基因组编辑蛋白递送载体的组合合成策略

Zhang, Jianye; Hołubowicz, Rafał; Smidak, Roman; Hu, Yulun; Du, Samuel W; Felgner, Jiin H; Palczewska, Grazyna; Rodrigues Menezes, Carolline; Risaliti, Eleonora; Dong, Zhiqian; Ma, Xiuli; Shayegan, Mojtaba H; Chen, Paul Z; Xing, Li; Hołubowicz, Maria; Li, Bowen; Liu, David R; Felgner, Philip L; Tochtrop, Gregory P; Palczewski, Krzysztof

Mechanistic machine learning enables interpretable and generalizable prediction of prime editing outcomes

机制机器学习能够对主要编辑结果进行可解释且可推广的预测。

Hsu, Alvin; Chen, Peter J; Li, Angus H; Hemez, Colin F; Gao, Xin D; Terrey, Markus; Nelson, Charlie; Selvam, Vijay; Cristian, Ana; McElroy, Amber N; Steinbeck, Benjamin J; Mahadeshwar, Gandhar K; Pandey, Smriti; Barsdale, Zachary; Chen, Paul Z; Sousa, Alexander A; Sakai, Holt A; Silverstein, Rachel A; Morad, Ilias; Krueger, Ryan K; Shen, Max W; Kleinstiver, Benjamin P; Lutz, Cathleen M; Tolar, Jakub; Blazar, Bruce R; Osborn, Mark J; Liu, David R

Addressing the Clinical Workforce Shortage by Retaining the Tenured Laboratory Professionals

通过留住资深实验室专业人员来解决临床劳动力短缺问题

Chiou, Paul Z; Mulder, Lotte

Safer and efficient base editing and prime editing via ribonucleoproteins delivered through optimized lipid-nanoparticle formulations

通过优化的脂质纳米颗粒制剂递送核糖核蛋白,实现更安全高效的碱基编辑和先导编辑

Rafał Hołubowicz #,Samuel W Du #,Jiin Felgner #,Roman Smidak,Elliot H Choi,Grazyna Palczewska,Carolline Rodrigues Menezes,Zhiqian Dong,Fangyuan Gao,Omar Medani,Alexander L Yan,Maria W Hołubowicz,Paul Z Chen,Marco Bassetto,Eleonora Risaliti,David Salom,J Noah Workman,Philip D Kiser,Andrzej T Foik,David C Lyon,Gregory A Newby,David R Liu,Philip L Felgner,Krzysztof Palczewski

Blood-brain barrier crossing biopolymer targeting c-Myc and anti-PD-1 activate primary brain lymphoma immunity: Artificial intelligence analysis

靶向c-Myc和抗PD-1的血脑屏障穿透性生物聚合物激活原发性脑淋巴瘤免疫:人工智能分析

Ljubimov, Vladimir A; Sun, Tao; Wang, Jiawei; Li, Lian; Wang, Paul Z; Ljubimov, Alexander V; Holler, Eggehard; Black, Keith L; Kopeček, Jindřich; Ljubimova, Julia Y; Yang, Jiyuan

TIGER: A tdTomato in vivo genome-editing reporter mouse for investigating precision-editor delivery approaches

TIGER:一种用于研究精准编辑递送方法的tdTomato体内基因组编辑报告小鼠

Du, Samuel W; Palczewska, Grazyna; Dong, Zhiqian; Lauterborn, Julie C; Kaipa, Balasankara Reddy; Yan, Alexander L; Hołubowicz, Rafał; Ha, Siyoung; Chen, Paul Z; Gall, Christine M; Zode, Gulab; Liu, David R; Palczewski, Krzysztof

Markers of Early Liver Dysfunction Associate With Reduced Heart Rate Variability in Adolescents With Type 1 Diabetes

早期肝功能障碍标志物与1型糖尿病青少年心率变异性降低相关

Velayutham, Vallimayil; Benitez-Aguirre, Paul Z; Liew, Gerald; Jenkins, Alicia J; Craig, Maria E; Donaghue, Kim C

Performance of the multi-target hepatocellular carcinoma blood test: Design and rationale of the ALTUS study

多靶点肝细胞癌血液检测的性能:ALTUS 研究的设计和原理

John, Binu V; Camardo, Mark; Porter, Kyle; Elias, Paul Z; Kielar-Grevstad, Elle; Rego, Seema P; Parikh, Neehar D; Roberts, Lewis R; Silva, Alvin C; Singal, Amit G; Yang, Ju Dong; Limburg, Paul J

Analysis of ChatGPT Responses to Ophthalmic Cases: Can ChatGPT Think like an Ophthalmologist?

ChatGPT 对眼科病例的回答分析:ChatGPT 能像眼科医生一样思考吗?

Chen, Jimmy S; Reddy, Akshay J; Al-Sharif, Eman; Shoji, Marissa K; Kalaw, Fritz Gerald P; Eslani, Medi; Lang, Paul Z; Arya, Malvika; Koretz, Zachary A; Bolo, Kyle A; Arnett, Justin J; Roginiel, Aliya C; Do, Jiun L; Robbins, Shira L; Camp, Andrew S; Scott, Nathan L; Rudell, Jolene C; Weinreb, Robert N; Baxter, Sally L; Granet, David B

Paediatric Thyroid Carcinoma: The Genetic Revolution and Its Implications for Therapy and Outcomes

儿童甲状腺癌:基因革命及其对治疗和预后的影响

Vanderniet, Joel A; Fuentes-Bolanos, Noemi A; Cho, Yoon Hi; Tucker, Katherine M; Anazodo, Antoinette; Bauer, Andrew J; Benitez-Aguirre, Paul Z