Accelerated Endosomal Escape of Splice-Switching Oligonucleotides Enables Efficient Hepatic Splice Correction
加速剪接转换寡核苷酸的内体逃逸可实现有效的肝脏剪接校正
期刊:ACS Applied Materials & Interfaces
影响因子:8.3
doi:10.1021/acsami.4c19340
Silvia Weiss, Simon Decker, Christoph Kugler, Laura Bocanegra Gómez, Helene Fasching, Denise Benisch, Fatih Alioglu, Levente Ferencz, Theresa Birkfeld, Filip Ilievski, Volker Baumann, Alina Duran, Enes Dusinovic, Nadine Follrich, Sandra Milenkovic, Dajana Mihalicokova, Daniel Paunov, Karla Singeorza