日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Detailed Protocol for the Novel and Scalable Viral Vector Upstream Process for AAV Gene Therapy Manufacturing

用于AAV基因治疗生产的新型可扩展病毒载体上游工艺的详细方案

Selvaraj, Nagarathinam; Wang, Chao-Kuei; Bowser, Brian; Broadt, Trevor; Shaban, Samir; Burns, Jenna; Saptharishi, Nirmala; Pechan, Peter; Golebiowski, Diane; Alimardanov, Asaf; Yang, Nora; Mitra, George; Vepachedu, Ramarao

Gene Therapies for Neovascular Age-Related Macular Degeneration

基因疗法治疗新生血管性年龄相关性黄斑变性

Pechan, Peter; Wadsworth, Samuel; Scaria, Abraham

Aurintricarboxylic acid increases yield of HSV-1 vectors

金精三羧酸可提高HSV-1载体的产量

Pechan, Peter; Ardinger, Jeffery; Ketavarapu, Jyothi; Rubin, Hillard; Wadsworth, Samuel C; Scaria, Abraham

AAV5-mediated sFLT01 gene therapy arrests retinal lesions in Ccl2(-/-)/Cx3cr1(-/-) mice

AAV5介导的sFLT01基因疗法可阻止Ccl2(-/-)/Cx3cr1(-/-)小鼠的视网膜病变。

Tuo, Jingsheng; Pang, Ji-Jing; Cao, Xiaoguang; Shen, Defen; Zhang, Jun; Scaria, Abraham; Wadsworth, Samuel C; Pechan, Peter; Boye, Sanford L; Hauswirth, William W; Chan, Chi-Chao

Inhibition of choroidal neovascularization in a nonhuman primate model by intravitreal administration of an AAV2 vector expressing a novel anti-VEGF molecule.

在非人灵长类动物模型中,通过玻璃体内注射表达新型抗 VEGF 分子的 AAV2 载体抑制脉络膜新生血管形成

Lukason Michael, DuFresne Elizabeth, Rubin Hillard, Pechan Peter, Li Qiuhong, Kim Ivana, Kiss Szilard, Flaxel Christina, Collins Margaret, Miller Joan, Hauswirth William, Maclachlan Timothy, Wadsworth Samuel, Scaria Abraham