Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial
Acoramidis治疗转甲状腺素蛋白淀粉样变性心肌病的长期疗效:ATTRibute-CM随机临床试验的开放标签扩展研究
期刊:Jama Cardiology
影响因子:14.1
doi:10.1001/jamacardio.2026.0819
Soman, Prem; Cuddy, Sarah A M; Gillmore, Julian D; Sarswat, Nitasha; Judge, Daniel P; Cappelli, Francesco; Stern, Lily K; Wright, Richard; Akinboboye, Olakunle; Obici, Laura; Bhatt, Kunal; Xiong, Kuangnan; Castaño, Adam; Chen, Chris; Falvey, Heather; Pecoraro, Maria Lucia; Tamby, Jean-François; Sinha, Uma; Fox, Jonathan C; Shah, Keyur; Grodin, Justin L; Ambardekar, Amrut V; Alexander, Kevin M; Khouri, Michel G; Cheng, Richard K