日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Pharmacodynamics, Efficacy, and Safety of Intraputaminal Eladocagene Exuparvovec Administered to Pediatric Patients With Aromatic L-Amino Acid Decarboxylase Deficiency Using an MR-Compatible Cannula: 48 Weeks of Follow-Up

使用磁共振兼容套管对芳香族L-氨基酸脱羧酶缺乏症患儿进行壳核内注射Eladocagene Exuparvovec的药效学、疗效和安全性研究：48周随访

期刊:Journal of Inherited Metabolic Disease
影响因子:3.8
doi:10.1002/jimd.70151
Curry, Daniel J; Pearl, Phillip L; Stone, Scellig S D; Gilbert, Donald L; Vadivelu, Sudhakar; Ben-Zeev, Bruria; Vestal, Matthew; Zafar, Muhammad; Tai, Chun-Hwei; Chou, Sheng-Che; Zibly, Zion; Ungar, Lior; Parnes, Mered; Hull, Mariam; Emrick, Lisa; Werner, Christian; Krolick, Alexis; Penematsa, Vinay; Wang, Antonia; Rahman, Rezwanur; Golden, Lee; Chien, Yin-Hsiu; Hwu, Paul Wuh-Liang
发表日期：2026
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Confirmatory long-term efficacy and safety results of ataluren in patients with nmDMD from Study 041, an international, randomized, double-blind, placebo-controlled, Phase III trial

来自 041 研究的确认性长期疗效和安全性结果，该研究是一项国际性、随机、双盲、安慰剂对照的 III 期试验，旨在评估阿塔卢伦治疗非转移性杜氏肌营养不良症 (nmDMD) 患者的疗效和安全性。

期刊:Journal of Comparative Effectiveness Research
影响因子:2.5
doi:10.57264/cer-2024-0238
Vlodavets, Dmitry; Wu, Shiwen; Kostera-Pruszczyk, Anna; Chae, Jong-Hee; Gulati, Sheffali; Shin, Jin-Hong; Lorentzos, Michelle; Cairns, Anita; Jong, Yuh-Jyh; Komaki, Hirofumi; Statland, Jeffrey; de Queiroz Campos Araujo, Alexandra Prufer; Gurgel-Giannetti, Juliana; Takeshima, Yasuhiro; Escobar Cedillo, Rosa E; Karachunski, Peter; Haginoya, Kazuhiro; Penematsa, Vinay; Chou, Connie; Williams, Paula; Werner, Christian; McDonald, Craig M
DMD
发表日期：2025
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Ataluren delays loss of ambulation and respiratory decline in nonsense mutation Duchenne muscular dystrophy patients

阿塔卢伦可延缓无义突变杜氏肌营养不良症患者的行走能力丧失和呼吸功能衰退。

期刊:Journal of Comparative Effectiveness Research
影响因子:2.5
doi:10.2217/cer-2021-0196
McDonald, Craig M; Muntoni, Francesco; Penematsa, Vinay; Jiang, Joel; Kristensen, Allan; Bibbiani, Francesco; Goodwin, Elizabeth; Gordish-Dressman, Heather; Morgenroth, Lauren; Werner, Christian; Li, James; Able, Richard; Trifillis, Panayiota; Tulinius, Már
发表日期：2022
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How many clinic visits does it take to treat distal radial fractures?

治疗桡骨远端骨折需要多少次门诊就诊？

期刊:International Orthopaedics
影响因子:2.6
doi:10.1007/s00264-006-0282-9
Kumar, S; Penematsa, S R; Sadri, M; Deshmukh, S C
骨折
发表日期：2008
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Can radiological results be surrogate markers of functional outcome in distal radial extra-articular fractures?

放射学结果能否作为桡骨远端关节外骨折功能预后的替代指标？

期刊:International Orthopaedics
影响因子:2.6
doi:10.1007/s00264-007-0355-4
Kumar, Skand; Penematsa, Subbaraju; Sadri, Maziar; Deshmukh, Subodh C
骨折
发表日期：2008
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Are drains required following a routine primary total joint arthroplasty?

常规初次全关节置换术后是否需要放置引流管？

期刊:International Orthopaedics
影响因子:2.6
doi:10.1007/s00264-006-0245-1
Kumar, Skand; Penematsa, Subbaraju; Parekh, Sailesh
发表日期：2007
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