日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Retinal gene therapy for Stargardt disease with dual AAV intein vectors is both safe and effective in large animal models.

使用双AAV内含子载体的视网膜基因疗法治疗Stargardt病在大动物模型中安全有效

Ferla Rita, Pugni Eugenio, Lupo Mariangela, Tiberi Paola, Fioretto Federica, Perota Andrea, Duchi Roberto, Lagutina Irina, Gesualdo Carlo, Rossi Settimio, Ventrella Domenico, Elmi Alberto, McClinton Benjamin, Toomes Carmel, Xu Tongzhou, Molday Robert S, Surace Enrico M, Simonelli Francesca, Bacci Maria L, Galli Cesare, Memon Muhammad A, Shams Naveed, Auricchio Alberto, Trapani Ivana

Transabdominal ultrasound guided AAV9-GFP delivery in fetal pigs: a translational and minimally invasive model for in utero fetal gene therapy.

经腹部超声引导 AAV9-GFP 递送至胎猪:一种用于子宫内胎儿基因治疗的转化和微创模型。

Di Donfrancesco Alessia, Adelizzi Alessia, Giri Anastasia, Duchi Roberto, Boito Simona, Barandalla Maria, Massaro Giulia, Santanatoglia Chiara, Cappellozza Enrica, Perota Andrea, Di Meo Ivano, Tiranti Valeria, Bottani Emanuela, Galli Cesare, Persico Nicola, Brunetti Dario

Double transgenic neonatal porcine islets as an alternative source for beta cell replacement therapy.

双转基因新生猪胰岛作为β细胞替代疗法的替代来源

Mourad Nizar I, Perota Andrea, Xhema Daela, Duchi Roberto, Lagutina Irina, Galli Cesare, Gianello Pierre

Changes in glial cell activation and extracellular vesicles production precede the onset of disease symptoms in transgenic hSOD1G93A pigs

转基因 hSOD1G93A 猪的神经胶质细胞活化和细胞外囊泡产生的变化先于疾病症状的出现

Maria Teresa Golia, Roberto Frigerio, Susanna Pucci, Francesca Sironi, Cassandra Margotta, Laura Pasetto, Camilla Testori, Elena Berrone, Francesco Ingravalle, Marcella Chiari, Alessandro Gori, Roberto Duchi, Andrea Perota, Luca Bergamaschi, Antonio D'Angelo, Giulia Cagnotti, Cesare Galli, Cristiano

A Study of Sonodynamic Therapy of Melanoma C540 Cells in Vitro by Titania/Gold Nanoparticles

二氧化钛/金纳米粒子对黑色素瘤C540细胞进行体外声动力治疗的研究

Perota, Ghazale; Faghani-Eskandarkolaei, Parsa; Zahraie, Niloofar; Zare, Mohammad Hosein; Sattarahmady, Naghmeh

Unexpected impairment of INa underpins reentrant arrhythmias in a knock-in swine model of Timothy syndrome

意外的 INa 损伤是 Timothy 综合征敲入猪模型中折返性心律失常的基础

Andreu Porta-Sánchez #, Andrea Mazzanti #, Carmen Tarifa #, Deni Kukavica #, Alessandro Trancuccio #, Muhammad Mohsin, Elisa Zanfrini, Andrea Perota, Roberto Duchi, Kevin Hernandez-Lopez, Miguel Eduardo Jáuregui-Abularach, Valerio Pergola, Eugenio Fernandez, Rossana Bongianino, Elisa Tavazzani, Patr

LIS1, a glyco-humanized swine polyclonal anti-lymphocyte globulin, as a novel induction treatment in solid organ transplantation

LIS1,一种糖基化人源化猪多克隆抗淋巴细胞球蛋白,作为实体器官移植中的一种新型诱导治疗药物

Rousse, Juliette; Royer, Pierre-Joseph; Evanno, Gwénaëlle; Lheriteau, Elsa; Ciron, Carine; Salama, Apolline; Shneiker, Françoise; Duchi, Roberto; Perota, Andrea; Galli, Cesare; Cozzi, Emmanuele; Blancho, Gilles; Duvaux, Odile; Brouard, Sophie; Soulillou, Jean-Paul; Bach, Jean-Marie; Vanhove, Bernard

Differential Immune Response to Bioprosthetic Heart Valve Tissues in the α1,3Galactosyltransferase-Knockout Mouse Model

α1,3半乳糖基转移酶基因敲除小鼠模型对生物心脏瓣膜组织的差异免疫反应

Kelly Casós, Roger Llatjós, Arnau Blasco-Lucas, Sebastián G Kuguel, Fabrizio Sbraga, Cesare Galli, Vered Padler-Karavani, Thierry Le Tourneau, Marta Vadori, Andrea Perota, Jean-Christian Roussel, Tomaso Bottio, Emanuele Cozzi, Jean-Paul Soulillou, Manuel Galiñanes, Rafael Máñez, Cristina Costa

High neutralizing potency of swine glyco-humanized polyclonal antibodies against SARS-CoV-2

猪糖基化人源化多克隆抗体具有较高的抗 SARS-CoV-2 中和效力

Bernard Vanhove, Odile Duvaux, Juliette Rousse, Pierre-Joseph Royer, Gwénaëlle Evanno, Carine Ciron, Elsa Lheriteau, Laurent Vacher, Nadine Gervois, Romain Oger, Yannick Jacques, Sophie Conchon, Apolline Salama, Roberto Duchi, Irina Lagutina, Andrea Perota, Philippe Delahaut, Matthieu Ledure, Melody

High neutralizing potency of swine glyco-humanized polyclonal antibodies against SARS-CoV-2

猪源糖基化人源多克隆抗体对SARS-CoV-2具有高中和效力

Vanhove, Bernard; Duvaux, Odile; Rousse, Juliette; Royer, Pierre-Joseph; Evanno, Gwénaëlle; Ciron, Carine; Lheriteau, Elsa; Vacher, Laurent; Gervois, Nadine; Oger, Romain; Jacques, Yannick; Conchon, Sophie; Salama, Apolline; Duchi, Roberto; Lagutina, Irina; Perota, Andrea; Delahaut, Philippe; Ledure, Matthieu; Paulus, Melody; So, Ray T; Mok, Chris Ka-Pun; Bruzzone, Roberto; Bouillet, Marc; Brouard, Sophie; Cozzi, Emanuele; Galli, Cesare; Blanchard, Dominique; Bach, Jean-Marie; Soulillou, Jean-Paul