日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Factor VIII trafficking to CD4+ T cells shapes its immunogenicity and requires several types of antigen-presenting cells

因子VIII向CD4+ T细胞的转运决定了其免疫原性,并且需要多种类型的抗原呈递细胞。

Kaczmarek, Radoslaw; Piñeros, Annie R; Patterson, Paige E; Bertolini, Thais B; Perrin, George Q; Sherman, Alexandra; Born, Jameson; Arisa, Sreevani; Arvin, Matthew C; Kamocka, Malgorzata M; Martinez, Michelle M; Dunn, Kenneth W; Quinn, Sean M; Morris, Johnathan J; Wilhelm, Amelia R; Kaisho, Tsuneyasu; Munoz-Melero, Maite; Biswas, Moanaro; Kaplan, Mark H; Linnemann, Amelia K; George, Lindsey A; Camire, Rodney M; Herzog, Roland W

Update on clinical gene therapy for hemophilia

血友病临床基因治疗最新进展

Perrin, George Q; Herzog, Roland W; Markusic, David M

Regulatory T cells and TLR9 activation shape antibody formation to a secreted transgene product in AAV muscle gene transfer

在AAV肌肉基因转移中,调节性T细胞和TLR9激活影响针对分泌型转基因产物的抗体形成。

Herzog, Roland W; Cooper, Mario; Perrin, George Q; Biswas, Moanaro; Martino, Ashley T; Morel, Laurence; Terhorst, Cox; Hoffman, Brad E

Plasmacytoid and conventional dendritic cells cooperate in crosspriming AAV capsid-specific CD8(+) T cells

浆细胞样树突状细胞和常规树突状细胞协同作用,启动AAV衣壳特异性CD8(+) T细胞。

Rogers, Geoffrey L; Shirley, Jamie L; Zolotukhin, Irene; Kumar, Sandeep R P; Sherman, Alexandra; Perrin, George Q; Hoffman, Brad E; Srivastava, Arun; Basner-Tschakarjan, Etiena; Wallet, Mark A; Terhorst, Cox; Biswas, Moanaro; Herzog, Roland W

Oral Tolerance Induction in Hemophilia B Dogs Fed with Transplastomic Lettuce

用转基因生菜喂养的B型血友病犬的口服耐受性诱导

Herzog, Roland W; Nichols, Timothy C; Su, Jin; Zhang, Bei; Sherman, Alexandra; Merricks, Elizabeth P; Raymer, Robin; Perrin, George Q; Häger, Mattias; Wiinberg, Bo; Daniell, Henry

Effective gene therapy for haemophilic mice with pathogenic factor IX antibodies.

针对患有致病性 IX 因子抗体的血友病小鼠的有效基因疗法

Markusic David M, Hoffman Brad E, Perrin George Q, Nayak Sushrusha, Wang Xiaomei, LoDuca Paul A, High Katherine A, Herzog Roland W

Activation of the NF-kappaB pathway by adeno-associated virus (AAV) vectors and its implications in immune response and gene therapy

腺相关病毒(AAV)载体激活NF-κB通路及其在免疫反应和基因治疗中的意义

Jayandharan, Giridhara R; Aslanidi, George; Martino, Ashley T; Jahn, Stephan C; Perrin, George Q; Herzog, Roland W; Srivastava, Arun

Prevention and Reversal of Antibody Responses Against Factor IX in Gene Therapy for Hemophilia B

预防和逆转血友病B基因治疗中针对因子IX的抗体反应

Nayak, Sushrusha; Sarkar, Debalina; Perrin, George Q; Moghimi, Babak; Hoffman, Brad E; Zhou, Shangzhen; Byrne, Barry J; Herzog, Roland W