日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Actions of L-Glutamine vs. COVID-19 Suggest Additional Benefit in Sickle Cell Disease

L-谷氨酰胺对抗 COVID-19 的作用提示其对镰状细胞病可能具有额外益处

Maas, Andrew I R; Menon, David K; Manley, Geoffrey T; Abrams, Mathew; Åkerlund, Cecilia; Andelic, Nada; Aries, Marcel; Bashford, Tom; Bell, Michael J; Bodien, Yelena G; Brett, Benjamin L; Büki, András; Chesnut, Randall M; Citerio, Giuseppe; Clark, David; Clasby, Betony; Cooper, D Jamie; Czeiter, Endre; Czosnyka, Marek; Dams-O'Connor, Kristen; De Keyser, Véronique; Diaz-Arrastia, Ramon; Ercole, Ari; van Essen, Thomas A; Falvey, Éanna; Ferguson, Adam R; Figaji, Anthony; Fitzgerald, Melinda; Foreman, Brandon; Gantner, Dashiell; Gao, Guoyi; Giacino, Joseph; Gravesteijn, Benjamin; Guiza, Fabian; Gupta, Deepak; Gurnell, Mark; Haagsma, Juanita A; Hammond, Flora M; Hawryluk, Gregory; Hutchinson, Peter; van der Jagt, Mathieu; Jain, Sonia; Jain, Swati; Jiang, Ji-Yao; Kent, Hope; Kolias, Angelos; Kompanje, Erwin J O; Lecky, Fiona; Lingsma, Hester F; Maegele, Marc; Majdan, Marek; Markowitz, Amy; McCrea, Michael; Meyfroidt, Geert; Mikolić, Ana; Mondello, Stefania; Mukherjee, Pratik; Nelson, David; Nelson, Lindsay D; Newcombe, Virginia; Okonkwo, David; Orešič, Matej; Peul, Wilco; Pisică, Dana; Polinder, Suzanne; Ponsford, Jennie; Puybasset, Louis; Raj, Rahul; Robba, Chiara; Røe, Cecilie; Rosand, Jonathan; Schueler, Peter; Sharp, David J; Smielewski, Peter; Stein, Murray B; von Steinbüchel, Nicole; Stewart, William; Steyerberg, Ewout W; Stocchetti, Nino; Temkin, Nancy; Tenovuo, Olli; Theadom, Alice; Thomas, Ilias; Espin, Abel Torres; Turgeon, Alexis F; Unterberg, Andreas; Van Praag, Dominique; van Veen, Ernest; Verheyden, Jan; Vyvere, Thijs Vande; Wang, Kevin K W; Wiegers, Eveline J A; Williams, W Huw; Wilson, Lindsay; Wisniewski, Stephen R; Younsi, Alexander; Yue, John K; Yuh, Esther L; Zeiler, Frederick A; Zeldovich, Marina; Zemek, Roger; Bancos, I; Geer, E B; Castinetti, F; Feelders, R; Fleseriu, M; Pivonello, R; Reincke, M; Tabarin, A; Le Mouhaër, J; Stermenska, J; Maldonado, M; Biller, B M; Bhatt, Neel S; Sharma, Akshay; St. Martin, Andrew; Martens, Michael; Riches, Marcie L; Dandoy, Christopher E; Auletta, Jeffery J; Abdelaal, Mahmoud AZ; Abdelrahman, Dyala; Cengiz, Mahir; Yavuzer, Hakan; Yavuzer, Serap; Bien, Ivy; Bhuva, Preeti; Pham, Jessica V; Siu, Royal; Tang, Mengdi; Ward, Ashley; Goodrow, Jason; Ludlum, Peter; Stark, Charles W; Perrine, Susan P

A phase 2 study of HQK-1001, an oral fetal haemoglobin inducer, in β-thalassaemia intermedia

一项针对中间型β-地中海贫血患者的II期临床研究,评估口服胎儿血红蛋白诱导剂HQK-1001的疗效。

Inati, Adlette; Kahale, Mario; Perrine, Susan P; Chui, David H K; Taher, Ali T; Koussa, Suzanne; Abi Nasr, Therese; Abbas, Hussein A; Ghalie, Richard G

A randomized phase I/II trial of HQK-1001, an oral fetal globin gene inducer, in β-thalassaemia intermedia and HbE/β-thalassaemia

HQK-1001(一种口服胎儿珠蛋白基因诱导剂)治疗中间型 β-地中海贫血和 HbE/β-地中海贫血的随机 I/II 期试验

Fucharoen, Suthat; Inati, Adlette; Siritanaratku, Noppadol; Thein, Swee L; Wargin, William C; Koussa, Suzanne; Taher, Ali; Chaneim, Nattawara; Boosalis, Michael; Berenson, Ronald; Perrine, Susan P

Advances in Virus-Directed Therapeutics against Epstein-Barr Virus-Associated Malignancies

针对EB病毒相关恶性肿瘤的病毒靶向治疗进展

Ghosh, Sajal K; Perrine, Susan P; Faller, Douglas V

Butyrate histone deacetylase inhibitors

丁酸组蛋白去乙酰化酶抑制剂

Steliou, Kosta; Boosalis, Michael S; Perrine, Susan P; Sangerman, José; Faller, Douglas V

Erythroid Kruppel-like factor (EKLF) is recruited to the gamma-globin gene promoter as a co-activator and is required for gamma-globin gene induction by short-chain fatty acid derivatives

红细胞 Kruppel 样因子 (EKLF) 作为共激活因子被募集到 γ-珠蛋白基因启动子上,是短链脂肪酸衍生物诱导 γ-珠蛋白基因表达所必需的。

Perrine, Susan P; Mankidy, Rishikesh; Boosalis, Michael S; Bieker, James J; Faller, Douglas V

Short-chain fatty acids induce gamma-globin gene expression by displacement of a HDAC3-NCoR repressor complex

短链脂肪酸通过置换 HDAC3-NCoR 抑制复合物来诱导 γ-珠蛋白基因表达。

Mankidy, Rishikesh; Faller, Douglas V; Mabaera, Rodwell; Lowrey, Christopher H; Boosalis, Michael S; White, Gary L; Castaneda, Serguei A; Perrine, Susan P

Identification of novel small-molecule inducers of fetal hemoglobin using pharmacophore and 'PSEUDO' receptor models

利用药效团和“伪”受体模型鉴定新型胎儿血红蛋白小分子诱导剂

Bohacek, Regine; Boosalis, Michael S; McMartin, Colin; Faller, Douglas V; Perrine, Susan P

Short-chain fatty acid derivatives induce fetal globin expression and erythropoiesis in vivo.

短链脂肪酸衍生物可诱导胎儿珠蛋白表达和体内红细胞生成

Pace Betty S, White Gary L, Dover George J, Boosalis Michael S, Faller Douglas V, Perrine Susan P