Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells
高效 CRISPR/Cas9 介导编辑强直性肌营养不良症患者来源的 iPS 和成肌细胞中的三核苷酸重复扩增
期刊:Nucleic Acids Research
影响因子:16.6
doi:10.1093/nar/gky548
Sumitava Dastidar, Simon Ardui, Kshitiz Singh, Debanjana Majumdar, Nisha Nair, Yanfang Fu, Deepak Reyon, Ermira Samara, Mattia F M Gerli, Arnaud F Klein, Wito De Schrijver, Jaitip Tipanee, Sara Seneca, Warut Tulalamba, Hui Wang, Yoke Chin Chai, Peter In't Veld, Denis Furling, Francesco Saverio Tedes
